首页
学术期刊
论文检测
AIGC检测
热点
更多
数据
Estimation of Health Utility Scores for Glycogen Storage Disease Type Ia
被引:0
|
作者
:
Eliza Kruger
论文数:
0
引用数:
0
h-index:
0
机构:
Ultragenyx Pharmaceutical Inc.,
Eliza Kruger
Daniel Aggio
论文数:
0
引用数:
0
h-index:
0
机构:
Ultragenyx Pharmaceutical Inc.,
Daniel Aggio
Hayley de Freitas
论文数:
0
引用数:
0
h-index:
0
机构:
Ultragenyx Pharmaceutical Inc.,
Hayley de Freitas
Andrew Lloyd
论文数:
0
引用数:
0
h-index:
0
机构:
Ultragenyx Pharmaceutical Inc.,
Andrew Lloyd
机构
:
[1]
Ultragenyx Pharmaceutical Inc.,
[2]
Acaster Lloyd Consulting Ltd,undefined
来源
:
PharmacoEconomics - Open
|
2023年
/ 7卷
关键词
:
D O I
:
暂无
中图分类号
:
学科分类号
:
摘要
:
引用
收藏
页码:627 / 638
页数:11
相关论文
共 50 条
[41]
Canine model and genomic structural organization of glycogen storage disease type Ia (GSD Ia)
Kishnani, PS
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Div Med Genet, Durham, NC 27710 USA
Kishnani, PS
Faulkner, E
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Div Med Genet, Durham, NC 27710 USA
Faulkner, E
VanCamp, S
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Div Med Genet, Durham, NC 27710 USA
VanCamp, S
Jackson, M
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Div Med Genet, Durham, NC 27710 USA
Jackson, M
Brown, T
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Div Med Genet, Durham, NC 27710 USA
Brown, T
Boney, A
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Div Med Genet, Durham, NC 27710 USA
Boney, A
Koeberl, D
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Div Med Genet, Durham, NC 27710 USA
Koeberl, D
Chen, YT
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Div Med Genet, Durham, NC 27710 USA
Chen, YT
VETERINARY PATHOLOGY,
2001,
38
(01)
: 83
-
91
[42]
MORE ABOUT RENAL-DISEASE IN TYPE IA GLYCOGEN-STORAGE-DISEASE
DERITUERTO, STM
论文数:
0
引用数:
0
h-index:
0
机构:
HOSP GEN GALICIA, SERV MED INTERNA, SANTIAGO, SPAIN
DERITUERTO, STM
SANCHEZGUISANDE, D
论文数:
0
引用数:
0
h-index:
0
机构:
HOSP GEN GALICIA, SERV MED INTERNA, SANTIAGO, SPAIN
SANCHEZGUISANDE, D
FORTEZA, J
论文数:
0
引用数:
0
h-index:
0
机构:
HOSP GEN GALICIA, SERV MED INTERNA, SANTIAGO, SPAIN
FORTEZA, J
NOVOA, D
论文数:
0
引用数:
0
h-index:
0
机构:
HOSP GEN GALICIA, SERV MED INTERNA, SANTIAGO, SPAIN
NOVOA, D
ROMERO, R
论文数:
0
引用数:
0
h-index:
0
机构:
HOSP GEN GALICIA, SERV MED INTERNA, SANTIAGO, SPAIN
ROMERO, R
RODRIGUEZ, MI
论文数:
0
引用数:
0
h-index:
0
机构:
HOSP GEN GALICIA, SERV MED INTERNA, SANTIAGO, SPAIN
RODRIGUEZ, MI
BARRIO, E
论文数:
0
引用数:
0
h-index:
0
机构:
HOSP GEN GALICIA, SERV MED INTERNA, SANTIAGO, SPAIN
BARRIO, E
NEPHRON,
1992,
62
(04):
: 477
-
478
[43]
Efficacy of Genome Editing in Infant Mice with Glycogen Storage Disease Type Ia
Arnson, Benjamin
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Sch Med, Durham, NC USA
Duke Univ, Sch Med, Durham, NC USA
Arnson, Benjamin
Li, Songtao
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Sch Med, Durham, NC USA
Duke Univ, Sch Med, Durham, NC USA
Li, Songtao
Gheorgiu, Dorothy
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Sch Med, Durham, NC USA
Duke Univ, Sch Med, Durham, NC USA
Gheorgiu, Dorothy
Brooks, Elizabeth
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Sch Med, Durham, NC USA
Duke Univ, Sch Med, Durham, NC USA
Brooks, Elizabeth
Han, Sang-Oh
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Sch Med, Durham, NC USA
Duke Univ, Sch Med, Durham, NC USA
Han, Sang-Oh
Ilich, Ekaterina
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Sch Med, Durham, NC USA
Duke Univ, Sch Med, Durham, NC USA
Ilich, Ekaterina
Cullen, Bryan R.
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Sch Med, Durham, NC USA
Duke Univ, Sch Med, Durham, NC USA
Cullen, Bryan R.
Koeberl, Dwight D.
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Sch Med, Durham, NC USA
Duke Univ, Sch Med, Durham, NC USA
Koeberl, Dwight D.
MOLECULAR THERAPY,
2022,
30
(04)
: 115
-
116
[44]
Bezafibrate Enhances AAV Gene Therapy in Glycogen Storage Disease Type Ia
Kang, Hye Ri
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Durham, NC USA
Duke Univ, Durham, NC USA
Kang, Hye Ri
Waskowicz, Lauren
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Durham, NC USA
Duke Univ, Durham, NC USA
Waskowicz, Lauren
Koeberl, Dwight D.
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Durham, NC USA
Duke Univ, Durham, NC USA
Koeberl, Dwight D.
MOLECULAR THERAPY,
2018,
26
(05)
: 447
-
447
[45]
Hepatic mitochondrial dysfunction is a feature of Glycogen Storage Disease Type Ia (GSDIa)
Benjamin L. Farah
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Benjamin L. Farah
Rohit A. Sinha
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Rohit A. Sinha
Yajun Wu
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Yajun Wu
Brijesh K. Singh
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Brijesh K. Singh
Andrea Lim
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Andrea Lim
Masahiro Hirayama
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Masahiro Hirayama
Dustin J. Landau
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Dustin J. Landau
Boon Huat Bay
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Boon Huat Bay
Dwight D. Koeberl
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Dwight D. Koeberl
Paul M. Yen
论文数:
0
引用数:
0
h-index:
0
机构:
Cardiovascular and Metabolic Disorders Program,Department of Anatomy
Paul M. Yen
Scientific Reports,
7
[46]
GLYCOGEN-STORAGE-DISEASE TYPE IA IN 2 LITTERMATE MALTESE PUPPIES
BRIX, AE
论文数:
0
引用数:
0
h-index:
0
机构:
DUKE UNIV,MED CTR,DEPT PEDIAT,DURHAM,NC 27710
BRIX, AE
HOWERTH, EW
论文数:
0
引用数:
0
h-index:
0
机构:
DUKE UNIV,MED CTR,DEPT PEDIAT,DURHAM,NC 27710
HOWERTH, EW
MCCONKIEROSELL, A
论文数:
0
引用数:
0
h-index:
0
机构:
DUKE UNIV,MED CTR,DEPT PEDIAT,DURHAM,NC 27710
MCCONKIEROSELL, A
PETERSON, D
论文数:
0
引用数:
0
h-index:
0
机构:
DUKE UNIV,MED CTR,DEPT PEDIAT,DURHAM,NC 27710
PETERSON, D
EGNOR, D
论文数:
0
引用数:
0
h-index:
0
机构:
DUKE UNIV,MED CTR,DEPT PEDIAT,DURHAM,NC 27710
EGNOR, D
WELLS, MR
论文数:
0
引用数:
0
h-index:
0
机构:
DUKE UNIV,MED CTR,DEPT PEDIAT,DURHAM,NC 27710
WELLS, MR
CHEN, YT
论文数:
0
引用数:
0
h-index:
0
机构:
DUKE UNIV,MED CTR,DEPT PEDIAT,DURHAM,NC 27710
CHEN, YT
VETERINARY PATHOLOGY,
1995,
32
(05)
: 460
-
465
[47]
Prenatal diagnosis of glycogen storage disease type Ia by restriction enzyme digestion
Trioche, P
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Antoine Beclere, Serv Pediat, F-92141 Clamart, France
Trioche, P
Francoual, J
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Antoine Beclere, Serv Pediat, F-92141 Clamart, France
Francoual, J
Audibert, F
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Antoine Beclere, Serv Pediat, F-92141 Clamart, France
Audibert, F
Chalas, J
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Antoine Beclere, Serv Pediat, F-92141 Clamart, France
Chalas, J
Lindenbaum, A
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Antoine Beclere, Serv Pediat, F-92141 Clamart, France
Lindenbaum, A
Odièvre, M
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Antoine Beclere, Serv Pediat, F-92141 Clamart, France
Odièvre, M
Labrune, P
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Antoine Beclere, Serv Pediat, F-92141 Clamart, France
Labrune, P
PRENATAL DIAGNOSIS,
1998,
18
(06)
: 629
-
631
[48]
Efficacy of gene therapy in canine glycogen storage disease type IA.
Pinto, C. R.
论文数:
0
引用数:
0
h-index:
0
机构:
N Carolina State Univ, Coll Vet Med, Raleigh, NC 27695 USA
Pinto, C. R.
Brown, T. R.
论文数:
0
引用数:
0
h-index:
0
机构:
N Carolina State Univ, Coll Vet Med, Raleigh, NC 27695 USA
Brown, T. R.
Vaughn, V.
论文数:
0
引用数:
0
h-index:
0
机构:
N Carolina State Univ, Coll Vet Med, Raleigh, NC 27695 USA
Vaughn, V.
Bird, A.
论文数:
0
引用数:
0
h-index:
0
机构:
N Carolina State Univ, Coll Vet Med, Raleigh, NC 27695 USA
Bird, A.
Sun, B. D.
论文数:
0
引用数:
0
h-index:
0
机构:
N Carolina State Univ, Coll Vet Med, Raleigh, NC 27695 USA
Sun, B. D.
Koeberl, D. D.
论文数:
0
引用数:
0
h-index:
0
机构:
N Carolina State Univ, Coll Vet Med, Raleigh, NC 27695 USA
Koeberl, D. D.
JOURNAL OF VETERINARY INTERNAL MEDICINE,
2007,
21
(03)
: 606
-
606
[49]
Gouty tendinitis revealing glycogen storage disease Type Ia in two adolescents
Carvès, C
论文数:
0
引用数:
0
h-index:
0
机构:
Grp Hosp Havre, Dept Pediat, Le Havre, France
Carvès, C
Duquenoy, A
论文数:
0
引用数:
0
h-index:
0
机构:
Grp Hosp Havre, Dept Pediat, Le Havre, France
Duquenoy, A
Toutain, F
论文数:
0
引用数:
0
h-index:
0
机构:
Grp Hosp Havre, Dept Pediat, Le Havre, France
Toutain, F
Trioche, P
论文数:
0
引用数:
0
h-index:
0
机构:
Grp Hosp Havre, Dept Pediat, Le Havre, France
Trioche, P
Zarnitski, C
论文数:
0
引用数:
0
h-index:
0
机构:
Grp Hosp Havre, Dept Pediat, Le Havre, France
Zarnitski, C
Le Roux, P
论文数:
0
引用数:
0
h-index:
0
机构:
Grp Hosp Havre, Dept Pediat, Le Havre, France
Le Roux, P
Le Luyer, B
论文数:
0
引用数:
0
h-index:
0
机构:
Grp Hosp Havre, Dept Pediat, Le Havre, France
Grp Hosp Havre, Dept Pediat, Le Havre, France
Le Luyer, B
JOINT BONE SPINE,
2003,
70
(02)
: 149
-
153
[50]
Hepatocellular adenoma and metabolic balance in patients with type Ia glycogen storage disease
Di Rocco, Maia
论文数:
0
引用数:
0
h-index:
0
机构:
Gaslini Inst, Pediat Div 2, Unit Rare Dis, I-16147 Genoa, Italy
Gaslini Inst, Pediat Div 2, Unit Rare Dis, I-16147 Genoa, Italy
Di Rocco, Maia
Calevo, Maria Grazia
论文数:
0
引用数:
0
h-index:
0
机构:
Gaslini Inst, Serv Epidemiol & Stat, I-16147 Genoa, Italy
Gaslini Inst, Pediat Div 2, Unit Rare Dis, I-16147 Genoa, Italy
Calevo, Maria Grazia
Taro, Marina
论文数:
0
引用数:
0
h-index:
0
机构:
Gaslini Inst, Pediat Div 2, Unit Rare Dis, I-16147 Genoa, Italy
Gaslini Inst, Pediat Div 2, Unit Rare Dis, I-16147 Genoa, Italy
Taro, Marina
Melis, Daniela
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Naples Federico 2, Pediat Clin, Naples, Italy
Gaslini Inst, Pediat Div 2, Unit Rare Dis, I-16147 Genoa, Italy
Melis, Daniela
Allegri, Anna Elsa Maria
论文数:
0
引用数:
0
h-index:
0
机构:
Gaslini Inst, Pediat Div 2, Unit Rare Dis, I-16147 Genoa, Italy
Gaslini Inst, Pediat Div 2, Unit Rare Dis, I-16147 Genoa, Italy
Allegri, Anna Elsa Maria
Parenti, Giancarlo
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Naples Federico 2, Pediat Clin, Naples, Italy
Gaslini Inst, Pediat Div 2, Unit Rare Dis, I-16147 Genoa, Italy
Parenti, Giancarlo
MOLECULAR GENETICS AND METABOLISM,
2008,
93
(04)
: 398
-
402
←
1
2
3
4
5
→