共 50 条
- [33] Orphan medicinal products: assessment after 5 years of European legislation M S-MEDECINE SCIENCES, 2006, 22 (01): : 71 - 74
- [34] Off-label use of orphan medicinal products: a Belgian qualitative study Orphanet Journal of Rare Diseases, 11
- [35] Development and validation of COMPASS: clinical evidence of orphan medicinal products – an assessment tool Orphanet Journal of Rare Diseases, 8
- [37] Trends in orphan medicinal products approvals in the European Union between 2010–2022 Orphanet Journal of Rare Diseases, 19
- [38] European regulation on orphan medicinal products: 10 years of experience and future perspectives Nature Reviews Drug Discovery, 2011, 10 : 341 - 349
- [40] Development and validation of COMPASS: clinical evidence of orphan medicinal products - an assessment tool ORPHANET JOURNAL OF RARE DISEASES, 2013, 8