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- [21] An Economic Evaluation of Voretigene Neparvovec for the Treatment of Biallelic RPE65-Mediated Inherited Retinal Dystrophies in the UKAdvances in Therapy, 2020, 37 : 1233 - 1247Daniel Viriato论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG,Natalie Bennett论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG,Raisa Sidhu论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG,Elizabeth Hancock论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG,Hannah Lomax论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG,David Trueman论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG,Robert E. MacLaren论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG,
- [22] Voretigene neparvovec for inherited retinal dystrophy due to RPE65 mutations: a scoping review of eligibility and treatment challenges from clinical trials to real practiceEYE, 2024, 38 (13) : 2504 - 2515Testa, Francesco论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, ItalyBacci, Giacomo论文数: 0 引用数: 0 h-index: 0机构: Meyer Childrens Hosp IRCCS, Pediat Ophthalmol Unit, Florence, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, ItalyFalsini, Benedetto论文数: 0 引用数: 0 h-index: 0机构: Univ Cattolica Sacro Cuore, Rome, Italy Fdn Policlin Univ A Gemelli IRCCS, UOC Oftalmol, Rome, Italy Bambino Gesu IRCCS Childrens Hosp, Dept Ophthalmol, Rome, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, ItalyIarossi, Giancarlo论文数: 0 引用数: 0 h-index: 0机构: Bambino Gesu IRCCS Childrens Hosp, Dept Ophthalmol, Rome, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, ItalyMelillo, Paolo论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, ItalyMucciolo, Dario Pasquale论文数: 0 引用数: 0 h-index: 0机构: S Jacopo Hosp, Ophthalmol Unit, Pistoia, Italy Univ Florence, Dept Neurosci Psychol Drug Res & Child Hlth, Florence, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, Italy论文数: 引用数: h-index:机构:Salvetti, Anna Paola论文数: 0 引用数: 0 h-index: 0机构: Univ Milan, Luigi Sacco Hosp, Dept Biomed & Clin Sci, Eye Clin, Milan, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, ItalySodi, Andrea论文数: 0 引用数: 0 h-index: 0机构: Univ Florence, Dept Neurosci Psychol Drug Res & Child Hlth, Florence, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, ItalyStaurenghi, Giovanni论文数: 0 引用数: 0 h-index: 0机构: Univ Milan, Luigi Sacco Hosp, Dept Biomed & Clin Sci, Eye Clin, Milan, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, ItalySimonelli, Francesca论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Naples, Italy
- [23] Efficacy, Safety, and Durability of Voretigene Neparvovec-rzyl in RPE65 Mutation-Associated Inherited Retinal Dystrophy Results of Phase 1 and 3 TrialsOPHTHALMOLOGY, 2019, 126 (09) : 1273 - 1285Maguire, Albert M.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut Inc, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USARussell, Stephen论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Inst Vis Res, Dept Ophthalmol & Visual Sci, Iowa City, IA USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAWellman, Jennifer A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut Inc, Philadelphia, PA 19104 USA Spark Therapeut Inc, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAChung, Daniel C.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut Inc, Philadelphia, PA 19104 USA Spark Therapeut Inc, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAYu, Zi-Fan论文数: 0 引用数: 0 h-index: 0机构: Stat Collaborat Inc, Washington, DC USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USATillman, Amy论文数: 0 引用数: 0 h-index: 0机构: Stat Collaborat Inc, Washington, DC USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAWittes, Janet论文数: 0 引用数: 0 h-index: 0机构: Stat Collaborat Inc, Washington, DC USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAPappas, Julie论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Westat Biostat & Data Management Core, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAElci, Okan论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Westat Biostat & Data Management Core, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAMarshall, Kathleen A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut Inc, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAMcCague, Sarah论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut Inc, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAReichert, Hannah论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa Hlth Care, Iowa City, IA USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USADavis, Maria论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa Hlth Care, Iowa City, IA USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USASimonelli, Francesca论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, Italy Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USALeroy, Bart P.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut Inc, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Ophthalmol, Philadelphia, PA 19104 USA Ghent Univ Hosp, Dept Ophthalmol, Ghent, Belgium Ghent Univ Hosp, Ctr Med Genet Ghent, Ghent, Belgium Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAWright, J. Fraser论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut Inc, Philadelphia, PA 19104 USA Spark Therapeut Inc, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USAHigh, Katherine A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut Inc, Philadelphia, PA 19104 USA Spark Therapeut Inc, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USABennett, Jean论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut Inc, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Ophthalmol, 51 North 39th St, Philadelphia, PA 19104 USA
- [24] Impact of Voretigene Neparvovec on Legal Blindness in Germany in Patients with RPE65 Mutation-Associated Inherited Retinal Dystrophy - Post Hoc Analysis of Phase III Trial DataINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2019, 60 (09)Lacey, Sue论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG, Basel, Switzerland Novartis Pharma AG, Basel, SwitzerlandAouadj, Celia论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG, Basel, Switzerland Novartis Pharma AG, Basel, SwitzerlandChung, Daniel C.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, Philadelphia, PA USA Novartis Pharma AG, Basel, SwitzerlandReape, Kathleen Z.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, Philadelphia, PA USA Novartis Pharma AG, Basel, SwitzerlandHigh, Katherine A.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, Philadelphia, PA USA Novartis Pharma AG, Basel, SwitzerlandViriato, Daniel论文数: 0 引用数: 0 h-index: 0机构: Novartis Pharma AG, Basel, Switzerland Novartis Pharma AG, Basel, Switzerland
- [25] Five-Year Post-Injection Results of the Phase 3 Trial of Voretigene Neparvovec-rzyl in Biallelic RPE65 Mutation-Associated Inherited Retinal DiseaseINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2021, 62 (08)Bennett, Jean论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Ophthalmol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USARussell, Stephen R.论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Iowa City, IA USA Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USAHigh, Katherine A.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, Philadelphia, PA USA Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USADrack, Arlene V.论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Iowa City, IA USA Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USAYu, Zi-Fan论文数: 0 引用数: 0 h-index: 0机构: Stat Collaborat Inc, Washington, DC USA Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USAChung, Daniel C.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, Philadelphia, PA USA Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USAReape, Kathy论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, Philadelphia, PA USA Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USAMaguire, Albert M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Ophthalmol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USA
- [26] Chromatic pupillometry as an objective outcome to evaluate effects of Voretigene Neparvovec treatment in patients with RPE65-related inherited retinal dystrophiesINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2023, 64 (08)Testa, Francesco论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, ItalyMelillo, Paolo论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, ItalyDi Iorio, Valentina论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, ItalyCitro, Amelia论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, ItalyRossi, Settimio论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, ItalyDella Corte, MIchele论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, ItalySimonelli, Francesca论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Naples, Italy
- [27] Visual function and retinal changes after voretigene neparvovec treatment in children with biallelic RPE65-related inherited retinal dystrophySCIENTIFIC REPORTS, 2022, 12 (01)Testa, Francesco论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, ItalyMelillo, Paolo论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, ItalyDi Iorio, Valentina论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, ItalyIovino, Claudio论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, ItalyFarinaro, Francesco论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, ItalyKarali, Marianthi论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy Univ Campania Luigi Vanvitelli, Dept Precis Med, Med Genet, Via Luigi De Crecchio 7, I-80138 Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, ItalyBanfi, Sandro论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Dept Precis Med, Med Genet, Via Luigi De Crecchio 7, I-80138 Naples, Italy Telethon Inst Genet & Med, Via Campi Flegrei 34, I-80078 Pozzuoli, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, ItalyRossi, Settimio论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, ItalyDella Corte, Michele论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, ItalySimonelli, Francesca论文数: 0 引用数: 0 h-index: 0机构: Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy Univ Campania Luigi Vanvitelli, Multidisciplinary Dept Med Surg & Dent Sci, Eye Clin, Via S Pansini 5,Bldg 15, I-80131 Naples, Italy
- [28] Visual function and retinal changes after voretigene neparvovec treatment in children with biallelic RPE65-related inherited retinal dystrophyScientific Reports, 12Francesco Testa论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental SciencesPaolo Melillo论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental SciencesValentina Di Iorio论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental SciencesClaudio Iovino论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental SciencesFrancesco Farinaro论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental SciencesMarianthi Karali论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental SciencesSandro Banfi论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental SciencesSettimio Rossi论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental SciencesMichele Della Corte论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental SciencesFrancesca Simonelli论文数: 0 引用数: 0 h-index: 0机构: University of Campania Luigi Vanvitelli,Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental Sciences
- [29] BUDGET IMPACT AND THE COST-EFFECTIVENESS OF INTRODUCING VORETIGENE NEPARVOVEC FOR TREATING INHERITED RETINAL DISEASES IN THE KINGDOM OF SAUDI ARABIAVALUE IN HEALTH, 2024, 27 (12) : S100 - S100Al Jedai, A.论文数: 0 引用数: 0 h-index: 0机构: Minist Hlth, Riyadh, Saudi Arabia Minist Hlth, Riyadh, Saudi ArabiaAL-Mudaiheem, H.论文数: 0 引用数: 0 h-index: 0机构: Minist Hlth, Riyadh, Saudi Arabia Minist Hlth, Riyadh, Saudi ArabiaBa-Abbad, R.论文数: 0 引用数: 0 h-index: 0机构: King Khalid Eye Specialist Hosp, Riyadh, Saudi Arabia Minist Hlth, Riyadh, Saudi ArabiaAlsulaiman, S.论文数: 0 引用数: 0 h-index: 0机构: King Khalid Eye Specialist Hosp, Riyadh, Saudi Arabia Minist Hlth, Riyadh, Saudi ArabiaAmro, S. A. A.论文数: 0 引用数: 0 h-index: 0机构: King Saud Univ, Riyadh, Saudi Arabia Minist Hlth, Riyadh, Saudi ArabiaAwad, N.论文数: 0 引用数: 0 h-index: 0机构: Carexso, Dubai, U Arab Emirates Minist Hlth, Riyadh, Saudi ArabiaOjeil, R.论文数: 0 引用数: 0 h-index: 0机构: Minist Hlth, Riyadh, Saudi Arabia
- [30] Year 2 results for a phase 3 trial of voretigene neparvovec in biallelic RPE65-mediated inherited retinal diseaseINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2017, 58 (08)Russell, Stephen R.论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa Hosp & Clin, Ophthalmol, Iowa City, IA 52242 USA Univ Iowa Hosp & Clin, Ophthalmol, Iowa City, IA 52242 USABennett, Jean论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Iowa Hosp & Clin, Ophthalmol, Iowa City, IA 52242 USAWellman, Jennifer A.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut, Philadelphia, PA USA Univ Iowa Hosp & Clin, Ophthalmol, Iowa City, IA 52242 USAChung, Daniel C.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut, Philadelphia, PA USA Univ Iowa Hosp & Clin, Ophthalmol, Iowa City, IA 52242 USAHigh, Katherine A.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut, Philadelphia, PA USA Univ Iowa Hosp & Clin, Ophthalmol, Iowa City, IA 52242 USAYu, Zi-Fan论文数: 0 引用数: 0 h-index: 0机构: Stat Collaborat Inc, Washington, DC USA Univ Iowa Hosp & Clin, Ophthalmol, Iowa City, IA 52242 USATillman, Amy论文数: 0 引用数: 0 h-index: 0机构: Stat Collaborat Inc, Washington, DC USA Univ Iowa Hosp & Clin, Ophthalmol, Iowa City, IA 52242 USAMaguire, Albert M.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Iowa Hosp & Clin, Ophthalmol, Iowa City, IA 52242 USA