Gene therapy protects heart in Friedreich's ataxia

被引:0
|
作者
Alexandra Flemming
机构
来源
关键词
D O I
暂无
中图分类号
学科分类号
摘要
引用
收藏
页码:417 / 417
相关论文
共 50 条
  • [41] Perspectives of the Friedreich ataxia community on gene therapy clinical trials
    Trantham, Shandra J.
    Coker, Mackenzi A.
    Norman, Samantha
    Crowley, Emma
    Berthy, Julie
    Byrne, Barry J.
    Subramony, Sub
    Lou, Xiangyang
    Corti, Manuela
    MOLECULAR THERAPY METHODS & CLINICAL DEVELOPMENT, 2024, 32 (01)
  • [42] Friedreich's ataxia
    Davies, GL
    BRITISH MEDICAL JOURNAL, 1940, 1940 : 192 - 192
  • [43] Autologous stem cell transplant with gene therapy for Friedreich ataxia
    Tajiri, Naoki
    Staples, Meaghan
    Kaneko, Yuji
    Kim, Seung U.
    Zesiewicz, Theresa A.
    Borlongan, Cesar V.
    MEDICAL HYPOTHESES, 2014, 83 (03) : 296 - 298
  • [44] Friedreich's ataxia
    Ortiz Uriarte, Ramon
    Garcia Ribes, Miguel
    Martin Gutierrez, V.
    Sorli, Jose V.
    Valderrama Zurian, Francisco Javier
    Mingarro Castillo, Maria Mercedes
    Ejarque Domenech, Ismael
    ATENCION PRIMARIA, 2009, 41 (06): : 339 - 341
  • [45] Epigenetic Therapy for Friedreich Ataxia
    Soragni, Elisabetta
    Miao, Wenyan
    Iudicello, Marco
    Jacoby, David
    De Mercanti, Stefania
    Clerico, Marinella
    Longo, Filomena
    Piga, Antonio
    Ku, Sherman
    Campau, Erica
    Du, Jintang
    Penalver, Pablo
    Rai, Myriam
    Madara, Joseph C.
    Nazor, Kristopher
    O'Connor, Melinda
    Maximov, Anton
    Loring, Jeanne F.
    Pandolfo, Massimo
    Durelli, Luca
    Gottesfeld, Joel M.
    Rusche, James R.
    ANNALS OF NEUROLOGY, 2014, 76 (04) : 489 - 508
  • [46] Rapid and Complete Reversal of Sensory Ataxia by Gene Therapy in a Novel Model of Friedreich Ataxia
    Piguet, Francoise
    de Montigny, Charline
    Vaucamps, Nadege
    Reutenauer, Laurence
    Eisenmann, Aurelie
    Puccio, Helene
    MOLECULAR THERAPY, 2018, 26 (08) : 1940 - 1952
  • [47] The heart in Friedreich's Ataxia: Basic findings and clinical implications
    Payne, R. Mark
    PROGRESS IN PEDIATRIC CARDIOLOGY, 2011, 31 (02) : 103 - 109
  • [48] Heart hypertrophy and function are improved by idebenone in Friedreich's ataxia
    Rustin, P
    Rötig, A
    Munnich, A
    Sidi, D
    FREE RADICAL RESEARCH, 2002, 36 (04) : 467 - 469
  • [49] Heart disease in Friedreich's ataxia: A clinical and echocardiographic study
    Gunal, N
    Saraclar, M
    Ozkutlu, S
    Senocak, F
    Topaloglu, H
    Karaaslan, S
    ACTA PAEDIATRICA JAPONICA, 1996, 38 (04): : 308 - 311
  • [50] Prevention and reversal of severe mitochondrial cardiomyopathy by gene therapy in a mouse model of Friedreich's ataxia
    Morgane Perdomini
    Brahim Belbellaa
    Laurent Monassier
    Laurence Reutenauer
    Nadia Messaddeq
    Nathalie Cartier
    Ronald G Crystal
    Patrick Aubourg
    Hélène Puccio
    Nature Medicine, 2014, 20 : 542 - 547