Primed for take-off

被引:0
|
作者
Philippe Leboulch
机构
[1] Philippe Leboulch is at the Institute of Emerging Diseases and Innovative Therapies,
[2] CEA,undefined
[3] INSERM,undefined
[4] University of Paris 11,undefined
[5] 92265 Fontenay-aux-Roses,undefined
[6] France. He is also at the Brigham & Women's Hospital and Harvard Medical School,undefined
[7] Boston,undefined
[8] Massachusetts,undefined
[9] USA.,undefined
来源
Nature | 2013年 / 500卷
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学科分类号
摘要
Gene therapy is finally getting a bumper crop of data that show clinical efficacy after fine-tuning of key parameters that control safety and potency. Supporting evidence comes from treatment of two life-threatening human diseases.
引用
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页码:280 / 282
页数:2
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