Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party

被引:0
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作者
Su Han Lum
Milen Minkov
Simon A. Jones
Sheree Hazelaar
Tiarlan Sirait
Jane E. Potter
Polina Stepensky
Frederic Garban
Herbert Pichler
Jerry Stein
Zuhre Kaya
Ansgar Schulz
Karin Mellgren
Cristina Diaz de Heredia
Cecile Pochon
Susana Riesco
Miguel Angel Diaz
Gérard Michel
Caroline Lindemans
Bernd Gruhn
Michael H. Albert
Arjan C. Lankester
Bénédicte Neven
Robert Wynn
机构
[1] Great North Children’s Hospital,Children’s Hematopoietic Stem Cell Transplant Unit
[2] Newcastle University,Translational and Clinical Research Institute
[3] Sigmund Freud University,Department of Bone Marrow Transplantation, Hadassah Hospital, Faculty of Medicine
[4] Willink Unit,CHU Grenoble Alpes
[5] St Mary’s Hospital,Department of Paediatrics
[6] EBMT Leiden Study Unit,Unit of Pediatric Hematology and Pediatric BMT
[7] Royal Manchester Children’s Hospital,Department of Pediatrics
[8] Hebrew University of Jerusalem,Department of Pediatric Oncology
[9] Université Grenoble Alpes,Pediatric Onco
[10] St. Anna Children’s Hospital,Hematology Department
[11] Medical University of Vienna,Department of Pediatrics
[12] Schneider Children’s Medical Center of Israel,Department of Pediatrics
[13] Gazi University School of Medicine,Department of Pediatrics
[14] University Medical Center Ulm,Willem
[15] Sahlgrenska University Hospital,Alexander Children’s Hospital, Pediatric Stem Cell Transplantation program
[16] Department of Pediatric Hematology and Oncology,Pediatric Hematology
[17] Hospital Universitari Vall d’Hebron,Immunology and Rheumatology Unit
[18] Nancy University Hospital,undefined
[19] Université de Lorraine,undefined
[20] Hospital Universitario de Salamanca,undefined
[21] Niño Jesus Children’s Hospital,undefined
[22] La Timone Children’s Hospital and Aix-Marseille University,undefined
[23] University Medical Center,undefined
[24] Utrecht,undefined
[25] Princess Máxima Center for Pediatric Oncology,undefined
[26] Jena University Hospital,undefined
[27] Dr. von Hauner University Children’s Hospital,undefined
[28] Ludwig-Maximilians-Universität,undefined
[29] Leiden University Medical Center,undefined
[30] Necker-Enfants Malades Hospital,undefined
[31] Assistance Publique—Hôpitaux de Paris (APHP),undefined
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页码:594 / 596
页数:2
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