Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party

被引：0

作者：

Su Han Lum

Milen Minkov

Simon A. Jones

Sheree Hazelaar

Tiarlan Sirait

Jane E. Potter

Polina Stepensky

Frederic Garban

Herbert Pichler

Jerry Stein

Zuhre Kaya

Ansgar Schulz

Karin Mellgren

Cristina Diaz de Heredia

Cecile Pochon

Susana Riesco

Miguel Angel Diaz

Gérard Michel

Caroline Lindemans

Bernd Gruhn

Michael H. Albert

Arjan C. Lankester

Bénédicte Neven

Robert Wynn

机构：

[1] Great North Children’s Hospital,Children’s Hematopoietic Stem Cell Transplant Unit

[2] Newcastle University,Translational and Clinical Research Institute

[3] Sigmund Freud University,Department of Bone Marrow Transplantation, Hadassah Hospital, Faculty of Medicine

[4] Willink Unit,CHU Grenoble Alpes

[5] St Mary’s Hospital,Department of Paediatrics

[6] EBMT Leiden Study Unit,Unit of Pediatric Hematology and Pediatric BMT

[7] Royal Manchester Children’s Hospital,Department of Pediatrics

[8] Hebrew University of Jerusalem,Department of Pediatric Oncology

[9] Université Grenoble Alpes,Pediatric Onco

[10] St. Anna Children’s Hospital,Hematology Department

[11] Medical University of Vienna,Department of Pediatrics

[12] Schneider Children’s Medical Center of Israel,Department of Pediatrics

[13] Gazi University School of Medicine,Department of Pediatrics

[14] University Medical Center Ulm,Willem

[15] Sahlgrenska University Hospital,Alexander Children’s Hospital, Pediatric Stem Cell Transplantation program

[16] Department of Pediatric Hematology and Oncology,Pediatric Hematology

[17] Hospital Universitari Vall d’Hebron,Immunology and Rheumatology Unit

[18] Nancy University Hospital,undefined

[19] Université de Lorraine,undefined

[20] Hospital Universitario de Salamanca,undefined

[21] Niño Jesus Children’s Hospital,undefined

[22] La Timone Children’s Hospital and Aix-Marseille University,undefined

[23] University Medical Center,undefined

[24] Utrecht,undefined

[25] Princess Máxima Center for Pediatric Oncology,undefined

[26] Jena University Hospital,undefined

[27] Dr. von Hauner University Children’s Hospital,undefined

[28] Ludwig-Maximilians-Universität,undefined

[29] Leiden University Medical Center,undefined

[30] Necker-Enfants Malades Hospital,undefined

[31] Assistance Publique—Hôpitaux de Paris (APHP),undefined

来源：

Bone Marrow Transplantation | 2023年 / 58卷

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引用

页码：594 / 596

页数：2

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[2] Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party
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