Population pharmacokinetics and pharmacodynamics of cysteamine in nephropathic cystinosis patients

被引：0
|
作者：
Naïm Bouazza
Jean-Marc Tréluyer
Chris Ottolenghi
Saik Urien
Georges Deschenes
Daniel Ricquier
Patrick Niaudet
Bernadette Chadefaux-Vekemans
机构：
[1] Université Paris Descartes,EA 3620
[2] AP-HP,Unité de Recherche clinique
[3] Hôpital Tarnier,Service de Pharmacologie Clinique
[4] AP-HP,CIC
[5] Hôpital Cochin-Saint-Vincent-de-Paul,0901 Inserm
[6] Cochin-Necker,Unité de Biochimie Métabolique
[7] Hôpital Necker-Enfants Malades,Service de Néphrologie Pédiatrique
[8] Hôpital Necker-Enfants Malades,Unité de Néphrologie Pédiatrique
[9] Hôpital Robert Debré,undefined
来源：
Orphanet Journal of Rare Diseases | / 6卷
关键词：
population pharmacokinetics; pharmacodynamics; cysteamine; cystinosis;
D O I：
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学科分类号：
摘要：
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