Trends in orphan medicinal products approvals in the European Union between 2010–2022

被引：0
|
作者：
Luísa Bouwman
Bruno Sepodes
Hubert Leufkens
Carla Torre
机构：
[1] Universidade de Lisboa,Faculdade de Farmácia
[2] Research Institute for Medicines of the University of Lisbon (iMED.ULisboa),Laboratory of Systems Integration Pharmacology, Clinical and Regulatory Science
[3] Utrecht University,Division of Pharmacoepidemiology and Clinical Pharmacology, Utrecht Institute for Pharmaceutical Sciences (UIPS)
来源：
Orphanet Journal of Rare Diseases | / 19卷
关键词：
Orphan regulation; Rare diseases; Orphan medicines; Accelerated assessment; Incentives;
D O I：
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摘要：
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