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- [21] Nusinersen in pediatric and adult patients with type III spinal muscular atrophyANNALS OF CLINICAL AND TRANSLATIONAL NEUROLOGY, 2021, 8 (08): : 1622 - 1634Pera, Maria Carmela论文数: 0 引用数: 0 h-index: 0机构: Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Ctr Clin Nemo, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyCoratti, Giorgia论文数: 0 引用数: 0 h-index: 0机构: Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Ctr Clin Nemo, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyBovis, Francesca论文数: 0 引用数: 0 h-index: 0机构: Univ Genoa, Dept Hlth Sci, Biostat Unit, Genoa, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyPane, Marika论文数: 0 引用数: 0 h-index: 0机构: Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Ctr Clin Nemo, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyPasternak, Amy论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyMontes, Jacqueline论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Neurol, Irving Med Ctr, New York, NY USA Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10027 USA Columbia Univ, Dept Rehabil & Regenerat Med, Irving Med Ctr, New York, NY USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalySansone, Valeria A.论文数: 0 引用数: 0 h-index: 0机构: Univ Milan, Niguarda Hosp, Neurorehabil Unit, Neuromuscular Omnictr Clin Ctr, Milan, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyDunaway Young, Sally论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Neurol, Palo Alto, CA 94304 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyDuong, Tina论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Neurol, Palo Alto, CA 94304 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, Italy论文数: 引用数: h-index:机构:Mizzoni, Irene论文数: 0 引用数: 0 h-index: 0机构: IRCCS Bambino Ges Childrens Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Disorders, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyD'Amico, Adele论文数: 0 引用数: 0 h-index: 0机构: IRCCS Bambino Ges Childrens Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Disorders, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyCivitello, Matthew论文数: 0 引用数: 0 h-index: 0机构: Univ Cent Florida, Coll Med, Nemours Childrens Hosp, Orlando, FL 32816 USA St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyGlanzman, Allan M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Dept Phys Therapy, Philadelphia, PA 19104 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyBruno, Claudio论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, Ctr Expt & Translat Myol, Genoa, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalySalmin, Francesca论文数: 0 引用数: 0 h-index: 0机构: Univ Milan, Niguarda Hosp, Neurorehabil Unit, Neuromuscular Omnictr Clin Ctr, Milan, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyMorando, Simone论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, Ctr Expt & Translat Myol, Genoa, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyDe Sanctis, Roberto论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ Agostino Gemelli IRCCS, Ctr Clin Nemo, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalySframeli, Maria论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, Dept Clin & Expt Med, Messina, Italy Univ Messina, Ctr Clin Nemo Sud, Messina, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyAntonaci, Laura论文数: 0 引用数: 0 h-index: 0机构: Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Ctr Clin Nemo, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyFrongia, Anna Lia论文数: 0 引用数: 0 h-index: 0机构: Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyRohwer, Annemarie论文数: 0 引用数: 0 h-index: 0机构: UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyScoto, Mariacristina论文数: 0 引用数: 0 h-index: 0机构: UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyDe Vivo, Darryl C.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Neurol, Irving Med Ctr, New York, NY USA Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10027 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyDarras, Basil T.论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyDay, John论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Neurol, Palo Alto, CA 94304 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyMartens, William论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, London, England Univ Rochester, Med Ctr, Rochester, NY 14642 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyPatanella, Katia A.论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ, Inst Neurol, Dept Neurosci, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyBertini, Enrico论文数: 0 引用数: 0 h-index: 0机构: IRCCS Bambino Ges Childrens Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Disorders, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyMuntoni, Francesco论文数: 0 引用数: 0 h-index: 0机构: UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England Great Ormond St Hosp Sick Children, London, England NIHR Great Ormond St Hosp, Biomed Res Ctr, London, England Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyFinkel, Richard论文数: 0 引用数: 0 h-index: 0机构: Univ Cent Florida, Coll Med, Nemours Childrens Hosp, Orlando, FL 32816 USA St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, ItalyMercuri, Eugenio论文数: 0 引用数: 0 h-index: 0机构: Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Ctr Clin Nemo, Rome, Italy Univ Cattolica Sacro Cuore, Pediat Neurol, Rome, Italy
- [22] Nusinersen Treatment in Adults With Spinal Muscular AtrophyNEUROLOGY-CLINICAL PRACTICE, 2021, 11 (03) : E317 - E327Duong, Tina论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAWolford, Connie论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAMcDermott, Michael P.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Med Ctr, Dept Biostat & Computat Biol, Rochester, NY 14627 USA Univ Rochester, Med Ctr, Dept Neurol, Rochester, NY 14627 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAMacpherson, Chelsea E.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Rehabil, Palo Alto, CA 94304 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAPasternak, Amy论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dept Neurol, Boston, MA USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAGlanzman, Allan M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Dept Neurol, Philadelphia, PA 19104 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAMartens, William B.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Med Ctr, Dept Neurol, Rochester, NY 14627 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAKichula, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Dept Neurol, Philadelphia, PA 19104 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USADarras, Basil T.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dept Neurol, Boston, MA USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USADe Vivo, Darryl C.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Neurol, New York, NY USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAZolkipli-Cunningham, Zarazuela论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Dept Neurol, Philadelphia, PA 19104 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAFinkel, Richard S.论文数: 0 引用数: 0 h-index: 0机构: Nemours Childrens Hosp, Dept Pediat, Orlando, FL USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USA论文数: 引用数: h-index:机构:Wintermark, Max论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Radiol, Palo Alto, CA 94304 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USASampson, Jacinda论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAHagerman, Katharine A.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USAYoung, Sally Dunaway论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USADay, John W.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USA Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USA
- [23] Nusinersen Treatment for Spinal Muscular Atrophy: Retrospective Multicenter Study of Pediatric and Adult Patients in KuwaitNEUROLOGY INTERNATIONAL, 2024, 16 (03): : 631 - 642AlTawari, Asma论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitZakaria, Mohammad论文数: 0 引用数: 0 h-index: 0机构: Al Adan Hosp, Dept Pediat, Hadiya 47000, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitKamel, Walaa论文数: 0 引用数: 0 h-index: 0机构: Ibn Sina Hosp, Neurol Dept, Shuwaikh Industrial 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitShaalan, Nayera论文数: 0 引用数: 0 h-index: 0机构: Ibn Sina Hosp, Neurol Dept, Shuwaikh Industrial 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitElghazawi, Gamal Ahmed Ismail论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitAli, Mohamed Esmat Anwar论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitSalota, Dalia论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitAttia, Amr论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitElanay, Ehab Elsayed Ali论文数: 0 引用数: 0 h-index: 0机构: Al Adan Hosp, Dept Pediat, Hadiya 47000, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitShalaby, Osama论文数: 0 引用数: 0 h-index: 0机构: Al Jahra Hosp, Dept Pediat, Al Jahra 003200, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitAlqallaf, Fatema论文数: 0 引用数: 0 h-index: 0机构: Mubarak Hosp, Pediat Dept, Neurol Unit, Jabriya 46300, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitMitic, Vesna论文数: 0 引用数: 0 h-index: 0机构: Al Farwaniya Hosp, Pediat Dept, Al Farwaniya 85000, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitBastaki, Laila论文数: 0 引用数: 0 h-index: 0机构: Kuwait Med Genet Ctr, Shuwaikh Industrial 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait
- [24] Effect of nusinersen treatment on quality of life and motor function in adult patients with spinal muscular atrophyNEUROMUSCULAR DISORDERS, 2024, 36 : 28 - 32Erdem, Nazan Simsek论文数: 0 引用数: 0 h-index: 0机构: Private Termessos Hosp, Dept Neurol, Konyaalti Antalya, Turkiye Private Termessos Hosp, Dept Neurol, Konyaalti Antalya, TurkiyeGencer, Gokce Yagmur Gunes论文数: 0 引用数: 0 h-index: 0机构: Akdeniz Univ, Fac Hlth Sci, Antalya, Turkiye Private Termessos Hosp, Dept Neurol, Konyaalti Antalya, Turkiye论文数: 引用数: h-index:机构:Uysal, Hilmi论文数: 0 引用数: 0 h-index: 0机构: Akdeniz Univ Hosp, Dept Neurol, TR-07070 Antalya, Turkiye Private Termessos Hosp, Dept Neurol, Konyaalti Antalya, Turkiye
- [25] Intrathecal nusinersen administration in adult spinal muscular atrophy patients with complex spinal anatomyTHERAPEUTIC ADVANCES IN NEUROLOGICAL DISORDERS, 2020, 13Cordts, Isabell论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyLingor, Paul论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyFriedrich, Benjamin论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Diagnost & Intervent Neuroradiol, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyPernpeintner, Verena论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyZimmer, Claus论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Diagnost & Intervent Neuroradiol, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyDeschauer, Marcus论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyMaegerlein, Christian论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Diagnost & Intervent Neuroradiol, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany
- [26] Safety of risdiplam in spinal muscular atrophy patients after short-term treatment with nusinersenMUSCLE & NERVE, 2024, 70 (05) : 1095 - 1098Yan, Yue论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R China Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R ChinaFeng, Yijie论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R China Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R ChinaJiang, Liya论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R China Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R ChinaJin, Jianing论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R China Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R ChinaMao, Shanshan论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R China Zhejiang Univ, Childrens Hosp, Natl Clin Res Ctr Child Hlth, Dept Neurol,Sch Med, Hangzhou 310052, Peoples R China
- [27] Nusinersen for spinal muscular atrophyTHERAPEUTIC ADVANCES IN NEUROLOGICAL DISORDERS, 2018, 11Wurster, Claudia D.论文数: 0 引用数: 0 h-index: 0Ludolph, Albert C.论文数: 0 引用数: 0 h-index: 0
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