NOVEL SMALL MOLECULE THERAPY FOR MUCOPOLYSACCHARIDOSIS TYPE I

被引：0
|
作者：
Bodamer, Olaf [1 ,2 ]
Brothers, Shaun [3 ,4 ]
Volmar, Claude-Henry [3 ,4 ]
Wahlestedt, Claes [3 ,4 ]
机构：
[1] Boston Childrens Hosp, BoLD Boston Childrens Lysosomal Storage Dis Progr, Boston, MA USA
[2] Boston Childrens Hosp, Div Genet & Genom, Boston, MA USA
[3] Univ Miami, Ctr Therapeut Innovat, Miami, FL USA
[4] Univ Miami, Dept Psychiat & Behav Sci, Miami, FL USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2016年 / 117卷 / 03期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
21
引用
收藏
页码：247 / 247
页数：1
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