A NOVEL, PLATFORMABLE APPROACH FOR THE REPRODUCIBLE AND SCALABLE ENRICHMENT OF FULL AAV CAPSIDS

被引:0
|
作者
Kavara, A. [1 ]
Boenning, K. [1 ]
Huato, J. [1 ]
Schofield, M. [2 ]
机构
[1] Pall Corp, R&D BioProc, Westborough, MA USA
[2] Pall, Bioproc R&D, Westborough, MA USA
关键词
AAV Purification; Full Capsid Enrichment;
D O I
暂无
中图分类号
Q813 [细胞工程];
学科分类号
摘要
616
引用
收藏
页码:S143 / S143
页数:1
相关论文
共 50 条
  • [41] Upstream Optimization Paved a Straightforward Path for High Percentage of Full Capsids in AAV6
    Fasano, James
    Hassaninasab, Azam
    Kennedy, Daniel
    Dao, Theresa
    Cai, Jay
    Matalka, Omar
    Beaudry, Christine
    Williams, Miranda
    Ponce, Lorenz
    Spooner, Arianna
    Sinclair, Emily
    Yin, Bojiao
    Segura, Maria Mercedes
    MOLECULAR THERAPY, 2023, 31 (04) : 222 - 223
  • [42] Novel AAV capsids show increased evasion to wild-type AAV9 neutralizing antibodies
    Kerns, S.
    Padegimas, L.
    Miller, T.
    HUMAN GENE THERAPY, 2019, 30 (11) : A119 - A119
  • [43] Rationally engineered novel AAV capsids for intra-articular gene delivery
    Li, Wenjun
    Feng, Susi Liu
    Herrschaft, Lizette
    Samulski, R. Jude
    Li, Chengwen
    MOLECULAR THERAPY METHODS & CLINICAL DEVELOPMENT, 2024, 32 (01)
  • [44] In Vivo Quantification Of Photoreceptor Transduction Efficiency Using Novel Modified AAV Capsids
    Ryals, Renee
    Kay, Christine
    Boye, Sanford
    Min, Seok-Hong
    Ayala, Andrea
    Hauswirth, William
    Boye, Shannon
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2013, 54 (15)
  • [45] LEOnto+: a scalable ontology enrichment approach
    Salma Sassi
    Anis Tissaoui
    Richard Chbeir
    World Wide Web, 2022, 25 : 2347 - 2378
  • [46] LEOnto+: a scalable ontology enrichment approach
    Sassi, Salma
    Tissaoui, Anis
    Chbeir, Richard
    WORLD WIDE WEB-INTERNET AND WEB INFORMATION SYSTEMS, 2022, 25 (06): : 2347 - 2378
  • [47] Novel AAV Capsids with Favorable Pre-Existing Immunity, Biodistribution, and In Vivo Potency
    Ramirez, Silvia
    Ishida, Justin
    Chen, Darlene
    Gebretsadik, Kahsay
    Leonard, Vincent
    Akeefe, Hassibullah
    Colosi, Peter
    Kumar, Sripriya Ravindra
    Agarwal, Pooja
    MOLECULAR THERAPY, 2024, 32 (04) : 257 - 257
  • [48] Novel AAV Capsids Display Expansive Transduction and Enhanced Potency in Subretinally Injected Mice
    Crosson, Sean M.
    Choudhury, Shreyasi
    Mellen, Russell
    Makal, Victoria
    Fajardo, Diego
    Peterson, James J.
    Zhang, Hangning
    Di Pasquale, Giovanni
    Chiorini, Jay A.
    Boye, Sanford L.
    Boye, Shannon E.
    MOLECULAR THERAPY, 2019, 27 (04) : 430 - 431
  • [49] Positron emission tomography imaging of novel AAV capsids maps rapid brain accumulation
    Seo, Jai Woong
    Ingham, Elizabeth S.
    Mahakian, Lisa
    Tumbale, Spencer
    Wu, Bo
    Aghevlian, Sadaf
    Shams, Shahin
    Baikoghli, Mo
    Jain, Poorva
    Ding, Xiaozhe
    Goeden, Nick
    Dobreva, Tatyana
    Flytzanis, Nicholas C.
    Chavez, Michael
    Singhal, Kratika
    Leib, Ryan
    James, Michelle L.
    Segal, David J.
    Cheng, R. Holland
    Silva, Eduardo A.
    Gradinaru, Viviana
    Ferrara, Katherine W.
    NATURE COMMUNICATIONS, 2020, 11 (01)
  • [50] Positron emission tomography imaging of novel AAV capsids maps rapid brain accumulation
    Jai Woong Seo
    Elizabeth S. Ingham
    Lisa Mahakian
    Spencer Tumbale
    Bo Wu
    Sadaf Aghevlian
    Shahin Shams
    Mo Baikoghli
    Poorva Jain
    Xiaozhe Ding
    Nick Goeden
    Tatyana Dobreva
    Nicholas C. Flytzanis
    Michael Chavez
    Kratika Singhal
    Ryan Leib
    Michelle L. James
    David J. Segal
    R. Holland Cheng
    Eduardo A. Silva
    Viviana Gradinaru
    Katherine W. Ferrara
    Nature Communications, 11