共 50 条
- [41] Upstream Optimization Paved a Straightforward Path for High Percentage of Full Capsids in AAV6MOLECULAR THERAPY, 2023, 31 (04) : 222 - 223Fasano, James论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USAHassaninasab, Azam论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USAKennedy, Daniel论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USADao, Theresa论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USACai, Jay论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USAMatalka, Omar论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USABeaudry, Christine论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USAWilliams, Miranda论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USAPonce, Lorenz论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USASpooner, Arianna论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USASinclair, Emily论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USAYin, Bojiao论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USASegura, Maria Mercedes论文数: 0 引用数: 0 h-index: 0机构: ElevateBio, Waltham, MA USA ElevateBio, Waltham, MA USA
- [42] Novel AAV capsids show increased evasion to wild-type AAV9 neutralizing antibodiesHUMAN GENE THERAPY, 2019, 30 (11) : A119 - A119Kerns, S.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut, Dallas, TX USA Abeona Therapeut, Dallas, TX USAPadegimas, L.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut, Dallas, TX USA Abeona Therapeut, Dallas, TX USAMiller, T.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut, Dallas, TX USA Abeona Therapeut, Dallas, TX USA
- [43] Rationally engineered novel AAV capsids for intra-articular gene deliveryMOLECULAR THERAPY METHODS & CLINICAL DEVELOPMENT, 2024, 32 (01)Li, Wenjun论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ N Carolina, Div Oral & Craniofacial Biomed, Adams Sch Dent, Chapel Hill, NC USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USAFeng, Susi Liu论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USAHerrschaft, Lizette论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USASamulski, R. Jude论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Dept Pharmacol, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USALi, Chengwen论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Dept Pediat, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Carolina Inst Dev Disabil, Chapel Hill, NC 27510 USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA
- [44] In Vivo Quantification Of Photoreceptor Transduction Efficiency Using Novel Modified AAV CapsidsINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2013, 54 (15)Ryals, Renee论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAKay, Christine论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USABoye, Sanford论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAMin, Seok-Hong论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAAyala, Andrea论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAHauswirth, William论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USABoye, Shannon论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USA
- [45] LEOnto+: a scalable ontology enrichment approachWorld Wide Web, 2022, 25 : 2347 - 2378Salma Sassi论文数: 0 引用数: 0 h-index: 0机构: University of Jendouba,VPNC Lab., FSJEGJAnis Tissaoui论文数: 0 引用数: 0 h-index: 0机构: University of Jendouba,VPNC Lab., FSJEGJRichard Chbeir论文数: 0 引用数: 0 h-index: 0机构: University of Jendouba,VPNC Lab., FSJEGJ
- [46] LEOnto+: a scalable ontology enrichment approachWORLD WIDE WEB-INTERNET AND WEB INFORMATION SYSTEMS, 2022, 25 (06): : 2347 - 2378Sassi, Salma论文数: 0 引用数: 0 h-index: 0机构: Univ Jendouba, FSJEGJ, VPNC Lab, Ave Maghreb Arabe, Jendouba 8189, Tunisia Univ Jendouba, FSJEGJ, VPNC Lab, Ave Maghreb Arabe, Jendouba 8189, TunisiaTissaoui, Anis论文数: 0 引用数: 0 h-index: 0机构: Univ Jendouba, FSJEGJ, VPNC Lab, Ave Maghreb Arabe, Jendouba 8189, Tunisia Univ Jendouba, FSJEGJ, VPNC Lab, Ave Maghreb Arabe, Jendouba 8189, TunisiaChbeir, Richard论文数: 0 引用数: 0 h-index: 0机构: Univ Pau & Pays Adour, E2S UPPA, LIUPPA, EA3000, Anglet, France Univ Jendouba, FSJEGJ, VPNC Lab, Ave Maghreb Arabe, Jendouba 8189, Tunisia
- [47] Novel AAV Capsids with Favorable Pre-Existing Immunity, Biodistribution, and In Vivo PotencyMOLECULAR THERAPY, 2024, 32 (04) : 257 - 257Ramirez, Silvia论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, San Rafael, CA USA BioMarin Pharmaceut Inc, San Rafael, CA USAIshida, Justin论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, San Rafael, CA USA BioMarin Pharmaceut Inc, San Rafael, CA USAChen, Darlene论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, San Rafael, CA USA BioMarin Pharmaceut Inc, San Rafael, CA USAGebretsadik, Kahsay论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, San Rafael, CA USA BioMarin Pharmaceut Inc, San Rafael, CA USALeonard, Vincent论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, San Rafael, CA USA BioMarin Pharmaceut Inc, San Rafael, CA USAAkeefe, Hassibullah论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, San Rafael, CA USA BioMarin Pharmaceut Inc, San Rafael, CA USAColosi, Peter论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, San Rafael, CA USA BioMarin Pharmaceut Inc, San Rafael, CA USAKumar, Sripriya Ravindra论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, San Rafael, CA USA BioMarin Pharmaceut Inc, San Rafael, CA USAAgarwal, Pooja论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, San Rafael, CA USA BioMarin Pharmaceut Inc, San Rafael, CA USA
- [48] Novel AAV Capsids Display Expansive Transduction and Enhanced Potency in Subretinally Injected MiceMOLECULAR THERAPY, 2019, 27 (04) : 430 - 431Crosson, Sean M.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAChoudhury, Shreyasi论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAMellen, Russell论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAMakal, Victoria论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAFajardo, Diego论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAPeterson, James J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USAZhang, Hangning论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USADi Pasquale, Giovanni论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Dent & Craniofacial Res, NIH, Bethesda, MD USA Univ Florida, Ophthalmol, Gainesville, FL USAChiorini, Jay A.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Dent & Craniofacial Res, NIH, Bethesda, MD USA Univ Florida, Ophthalmol, Gainesville, FL USABoye, Sanford L.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Pediat, Gainesville, FL USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USABoye, Shannon E.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Ophthalmol, Gainesville, FL USA Univ Florida, Ophthalmol, Gainesville, FL USA
- [49] Positron emission tomography imaging of novel AAV capsids maps rapid brain accumulationNATURE COMMUNICATIONS, 2020, 11 (01)Seo, Jai Woong论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USA Univ Calif Davis, Dept Biomed Engn, Davis, CA 95616 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAIngham, Elizabeth S.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Dept Biomed Engn, Davis, CA 95616 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAMahakian, Lisa论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Dept Biomed Engn, Davis, CA 95616 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USATumbale, Spencer论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAWu, Bo论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAAghevlian, Sadaf论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAShams, Shahin论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Dept Biomed Engn, Davis, CA 95616 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USABaikoghli, Mo论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Dept Mol & Cellular Biol, Davis, CA 95616 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAJain, Poorva论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USADing, Xiaozhe论文数: 0 引用数: 0 h-index: 0机构: CALTECH, Div Biol & Biol Engn, Pasadena, CA 91125 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAGoeden, Nick论文数: 0 引用数: 0 h-index: 0机构: CALTECH, Div Biol & Biol Engn, Pasadena, CA 91125 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USADobreva, Tatyana论文数: 0 引用数: 0 h-index: 0机构: CALTECH, Div Biol & Biol Engn, Pasadena, CA 91125 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAFlytzanis, Nicholas C.论文数: 0 引用数: 0 h-index: 0机构: CALTECH, Div Biol & Biol Engn, Pasadena, CA 91125 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAChavez, Michael论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Bioengn, Stanford, CA 94305 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USA论文数: 引用数: h-index:机构:Leib, Ryan论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ Mass Spectrometry, Stanford, CA USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAJames, Michelle L.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USASegal, David J.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Genome Ctr, Davis, CA 95616 USA Univ Calif Davis, Dept Biochem & Mol Med, Davis, CA 95616 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USACheng, R. Holland论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Dept Mol & Cellular Biol, Davis, CA 95616 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USASilva, Eduardo A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Dept Biomed Engn, Davis, CA 95616 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAGradinaru, Viviana论文数: 0 引用数: 0 h-index: 0机构: CALTECH, Div Biol & Biol Engn, Pasadena, CA 91125 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USAFerrara, Katherine W.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USA Stanford Univ, Dept Radiol, Sch Med, Mol Imaging Program Stanford MIPS, Stanford, CA 94305 USA
- [50] Positron emission tomography imaging of novel AAV capsids maps rapid brain accumulationNature Communications, 11Jai Woong Seo论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineElizabeth S. Ingham论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineLisa Mahakian论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineSpencer Tumbale论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineBo Wu论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineSadaf Aghevlian论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineShahin Shams论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineMo Baikoghli论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicinePoorva Jain论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineXiaozhe Ding论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineNick Goeden论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineTatyana Dobreva论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineNicholas C. Flytzanis论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineMichael Chavez论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineKratika Singhal论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineRyan Leib论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineMichelle L. James论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineDavid J. Segal论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineR. Holland Cheng论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineEduardo A. Silva论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineViviana Gradinaru论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of MedicineKatherine W. Ferrara论文数: 0 引用数: 0 h-index: 0机构: Stanford University,Molecular Imaging Program at Stanford (MIPS), Department of Radiology, School of Medicine