Autologous transplantation of human genome-edited hematopoietic stem cells for lysosomal storage disorders: the role of pre-transplant conditioning

被引：0
|
作者：
Gomez-Ospina, Natalia [1 ]
Colella, Pasqualina [1 ]
Khan, Shaukat [2 ]
Tomatsu, Shunji [2 ]
Poletto, Edina [3 ]
机构：
[1] Stanford Univ, Stanford, CA 94305 USA
[2] Nemours Alfred duPont Hosp, Wilmington, DE USA
[3] Hosp Clin Porto Alegre, Porto Alegre, RS, Brazil
来源：
MOLECULAR GENETICS AND METABOLISM | 2021年 / 132卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
OP089
引用
收藏
页码：S62 / S62
页数：1
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