Pyrukynd ushers in new era for rare cellular metabolic disease

被引：0
|
作者：
Harrison, Charlotte
机构：
[1] Canterbury, United Kingdom
来源：
NATURE BIOTECHNOLOGY | 2022年 / 40卷 / 04期
关键词：
D O I：
10.1038/s41587-022-01286-2
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
The approval of the first oral pill to treat a rare anemia heralds the arrival of a new class of agents that could shake up enzyme replacement therapies for metabolic disease.
引用
收藏
页码：448 / 448
页数：1
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