Development of gene therapy for haemophagocytic lymphohistiocytosis (HLH) due to perforin deficiency

被引:0
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作者
Carmo, M. [1 ]
Booth, C. [1 ]
Montiel-Equihua, C. A. [1 ]
Schambach, A. [2 ]
Baum, C. [2 ]
Thrasher, A. J. [1 ]
Gaspar, H. B. [1 ]
机构
[1] UCL, Inst Child Hlth, Mol Immunol Unit, London, England
[2] Hannover Med Sch, Dept Expt Hematol, D-3000 Hannover, Germany
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中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
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页码:1455 / 1455
页数:1
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