GCDH gene therapy shows efficacy in the glutaric aciduria type I mouse model.

被引：0
|
作者：
Mateu-Bosch, A. [1 ]
Gea-Sorli, S. [2 ]
Segur-Bailach, E. [1 ,2 ]
Garcia-Villoria, J. [1 ,2 ]
Ribes, A. [1 ,2 ]
Fillat, C. [1 ,2 ]
机构：
[1] IDIBAPS, Barcelona, Spain
[2] CIBERER, Barcelona, Spain
来源：
HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P246
引用
收藏
页码：A104 / A105
页数：2
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