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- [32] Correction of Wiskott-Aldrich syndrome by hematopoietic stem cell gene therapyHUMAN GENE THERAPY, 2010, 21 (10) : 1362 - 1363Boztug, Kaan论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanySchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Tumor Dis, Dept Translat Oncol, Heidelberg, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanySchwarzer, Adrian论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyBanerjee, Pinaki P.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Res Inst, Philadelphia, PA 19104 USA Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyBoehm, Marie论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyBeier, Rita论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyDiez, Ines Avedillo论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyDewey, Ricardo论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyBall, Claudia R.论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Tumor Dis, Dept Translat Oncol, Heidelberg, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyNowrouzi, Ali论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Tumor Dis, Dept Translat Oncol, Heidelberg, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyNaundorf, Sonja论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germany EUFETS AG, Idar Oberstein, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyKuehlcke, Klaus论文数: 0 引用数: 0 h-index: 0机构: EUFETS AG, Idar Oberstein, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyBlasczyk, Rainer论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Transfus Med, Hannover, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyRose, Martina论文数: 0 引用数: 0 h-index: 0机构: Minden Hosp, Dept Pediat, Minden, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyFraser, Chris论文数: 0 引用数: 0 h-index: 0机构: Royal Childrens Hosp, Queensland Childrens Canc Ctr, Parkville, Qld, Australia Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyLiesl, Mathias论文数: 0 引用数: 0 h-index: 0机构: Loma Linda Univ, Med Ctr, Dept Pediat Hematol & Oncol, Loma Linda, CA USA Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyFerrari, Rudolf论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Kemperhof, Koblenz, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyAbboud, Miguel论文数: 0 引用数: 0 h-index: 0机构: Amer Univ Beirut, Childrens Canc Ctr Lebanon, Beirut, Lebanon Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyAl-Herz, Waleed论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Allergy & Clin Immunol Unit, Dept Pediat, Kuwait, Kuwait Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyKondratenko, Irina论文数: 0 引用数: 0 h-index: 0机构: Russian Clin Childrens Hosp, Dept Clin Immunol, Moscow, Russia Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyMarodi, Laszlo论文数: 0 引用数: 0 h-index: 0机构: Univ Debrecen, Dept Infect & Pediat Immunol, Med & Hlth Sci Ctr, Debrecen, Hungary Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyOrange, Jordan S.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Res Inst, Philadelphia, PA 19104 USA Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germanyvon Kalle, Christof论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Tumor Dis, Dept Translat Oncol, Heidelberg, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, GermanyKlein, Christoph论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germany Hannover Med Sch, Dept Pediat Hematol Oncol, Hannover, Germany
- [33] Outcome of Hematopoietic Stem Cell Gene Therapy for Wiskott-Aldrich SyndromeBLOOD, 2019, 134Labrosse, Roxane论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAChu, Julia论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dana Farber Canc Inst, Boston, MA USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAArmant, Myriam论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAvan der Spek, Jet论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAMiggelbrink, Alexandra论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAFong, Johnson论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAEverett, John K.论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USARaymond, Hayley论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAKessler, Lyanna论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USADansereau, Colleen论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAMackinnon, Brenda论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAKoo, Stephanie论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAMorris, Emily论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USALondon, Wendy B.论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAOzen, Ahmet论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Istanbul, Turkey Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USABaris, Safa论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Istanbul, Turkey Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USADespotovic, Jenny M.论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Texas Childrens Hosp, Houston, TX 77030 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAForbes, Lisa论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Texas Childrens Hosp, Houston, TX 77030 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USASaitoh, Akihiko论文数: 0 引用数: 0 h-index: 0机构: Niigata Univ, Grad Sch Med & Dent Sci, Niigata, Japan Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USATakachi, Takayuki论文数: 0 引用数: 0 h-index: 0机构: Shizuoka Childrens Hosp, Dept Hematol & Oncol, Shizuoka, Japan Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAKing, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Hosp Ninos Luis Calvo Mackenna, Santiago, Chile Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAThi Mai Anh Thi Nguyen论文数: 0 引用数: 0 h-index: 0机构: City Childrens Hosp, Dept Hematol Oncol, Ho Chi Minh City, Vietnam Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAVy Do Uyen Vu论文数: 0 引用数: 0 h-index: 0机构: City Childrens Hosp, Dept Hematol Oncol, Ho Chi Minh City, Vietnam Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USABushman, Frederic D.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAGaly, Anne论文数: 0 引用数: 0 h-index: 0机构: Genethon, Evry, France Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USANotarangelo, Luigi论文数: 0 引用数: 0 h-index: 0机构: NIH, Bldg 10, Bethesda, MD 20892 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAWilliams, David A.论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USAPai, Sung-Yun论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USA Boston Childrens Hosp, Div Pediat Hematol Oncol, Boston, MA USA
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- [37] ISOLATION OF A NOVEL GENE MUTATED IN WISKOTT-ALDRICH SYNDROMECELL, 1994, 78 (04) : 635 - 644DERRY, JMJ论文数: 0 引用数: 0 h-index: 0机构: STANFORD UNIV, MED CTR, DEPT GENET, STANFORD, CA 94305 USAOCHS, HD论文数: 0 引用数: 0 h-index: 0机构: STANFORD UNIV, MED CTR, DEPT GENET, STANFORD, CA 94305 USAFRANCKE, U论文数: 0 引用数: 0 h-index: 0机构: STANFORD UNIV, MED CTR, DEPT GENET, STANFORD, CA 94305 USA
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