Safe Harbor Targeting of IL2RG Expression Cassettes for Gene Therapy of X-Linked Severe Combined Immunodeficiency (SCID-X1)

被引：0
|
作者：
Zhou, Sheng [1 ]
Ma, Zhijun [1 ]
Lu, Taihe [1 ]
Brimble, Mark A. [1 ]
Wang, Yong-Dong [1 ]
Davidoff, Andrew M. [1 ]
Sorrentino, Brian P. [1 ]
机构：
[1] St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA
来源：
MOLECULAR THERAPY | 2016年 / 24卷
关键词：
D O I：
10.1016/S1525-0016(16)33379-2
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
571
引用
收藏
页码：S228 / S228
页数：1
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