Translating RNAi Therapy for Spinocerebellar Ataxia 1 to the Clinic

被引：0
|
作者：
Keiser, Megan S. [1 ]
机构：
[1] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
来源：
MOLECULAR THERAPY | 2016年 / 24卷
关键词：
D O I：
10.1016/S1525-0016(16)33391-3
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
583
引用
收藏
页码：S232 / S232
页数：1
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