Development and Evaluation of Cone-Specific Promoters in Non-human Primates for Gene Therapy of Congenital Cone Diseases Including Achromatopsia

被引：0
|
作者：
Ye, Guo-jie [1 ]
Budzynski, Ewa [2 ]
Sonnentag, Peter [2 ]
Nork, Michael [3 ,4 ]
Sheibani, Nader [3 ,4 ]
Boye, Sanford L. [5 ]
Hauswirth, William W. [5 ]
Chulay, Jeffrey D. [1 ]
机构：
[1] AGTC, Alachua, FL USA
[2] Covance Labs Inc, Madison, WI USA
[3] Univ Wisconsin, Madison, WI USA
[4] OSOD LLC, Madison, WI USA
[5] Univ Florida, Gainesville, FL USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2014年 / 55卷 / 13期
关键词：
538 gene transfer/gene therapy; 648; photoreceptors; 688; retina;
D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
837
引用
收藏
页数：2
相关论文
共 50 条
  • [31] Adenovirus induced acute hepatitis in non-human primates after liver-directed gene therapy
    Lu, HY
    Sullivan, D
    Gerber, MA
    Dash, S
    CHINESE MEDICAL JOURNAL, 2002, 115 (05) : 726 - 731
  • [32] Evaluation of chimeric antigen receptor T cell therapy in non-human primates infected with SHIV or SIV
    Iwamoto, Nami
    Patel, Bhavik
    Song, Kaimei
    Mason, Rosemarie
    Bolivar-Wagers, Sara
    Bergamaschi, Cristina
    Pavlakis, George N.
    Berger, Edward
    Roederer, Mario
    PLOS ONE, 2021, 16 (03):
  • [33] Assessment of Clinical Feasibility of Image-Guided Liver Specific Hydrodynamic Gene Transfer in Non-Human Primates
    Kamimura, Kenya
    Kanefuji, Tsutomu
    Suda, Takeshi
    Yokoo, Takeshi
    Zhang, Guisheng
    Liu, Dexi
    MOLECULAR THERAPY, 2020, 28 (04) : 566 - 566
  • [34] Mechanistic Evaluation of Liver-Specific Transgene Repression from AAV Vectors in Non-Human Primates and Minipigs
    Wang, Zhuo
    Yang, Jason
    Qian, Randolph
    Qiao, Chunping
    Chen, Ting
    Clarke, Ryan
    Henry, William Marcus
    Nguyen, Trang
    Yost, Samantha
    Liu, Ye
    Danos, Olivier F.
    Bruder, Joseph T.
    Karumuthil-Melethil, Subha
    MOLECULAR THERAPY, 2023, 31 (04) : 135 - 135
  • [35] Development of a Platform for Parallel Functional Evaluation of Cell Type Specific Synthetic Promoters for Gene Therapy
    Kedaigle, Amanda J.
    Manchanda, Aayushi
    Sellon, Jonathan
    So, Kathy
    Xu, Pray
    Pregernig, Gabriela
    Gibson, Tyler M.
    Palermo, Adam
    Kowalczyk, Monika S.
    MOLECULAR THERAPY, 2023, 31 (04) : 225 - 225
  • [36] BIOSAFETY IN EX VIVO GENE THERAPY AND CONDITIONAL ABLATION OF LENTIVIRALLY-TRANSDUCED HEPATOCYTES IN NON-HUMAN PRIMATES
    Menzel, O.
    Birraux, J.
    Wildhaber, B.
    Jond, C.
    Lasne, F.
    Habre, W.
    Nguyen, T.
    Chardot, C.
    JOURNAL OF HEPATOLOGY, 2009, 50 : S17 - S18
  • [37] Gene therapy for cross-correction of somatic organs and the CNS in mucopolysaccharidosis II in rodents and non-human primates
    Chen, Nancy
    Ehmann, David E.
    Crooker, Robert
    Derakhchan, Katayoun
    Fang, Xiaodong
    Felice, Brian
    Galbreath, Elizabeth J.
    Glaus, Charles
    Gu, Hongbo
    Huang, Yan
    Li, Christine
    Li, Xing
    Liu, Nan
    Palmieri, Kathleen
    Simic, Damir
    Sypek, Joseph
    Thompson, Susan
    Winkelmann, Christopher T.
    Choi, Vivian W.
    MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2023, 29 : 286 - 302
  • [38] Efficacy and Safety of Liver-Directed Lentiviral Gene Therapy in Hemophilia B Dogs and Non-Human Primates
    Cantore, Alessio
    Milani, Michela
    Annoni, Andrea
    Liu, Tongyao
    Deschamps, Jack-Yves
    Ayuso, Eduard
    Nichols, Timothy
    Peters, Robert
    Naldini, Luigi
    MOLECULAR THERAPY, 2017, 25 (05) : 30 - 31
  • [39] Liver-Specific Transcriptional Modules Identified by Genome-Wide In Silico Analysis Enable Efficient Gene Therapy in Mice and Non-Human Primates
    Chuah, Marinee K.
    Petrus, Inge
    De Bleser, Pieter
    Le Guiner, Caroline
    Gernoux, Gwladys
    Adjali, Oumeya
    Nair, Nisha
    Willems, Jessica
    Evens, Hanneke
    Rincon, Melvin Y.
    Matrai, Janka
    Di Matteo, Mario
    Samara-Kuko, Ermira
    Yan, Bing
    Acosta-Sanchez, Abel
    Meliani, Amine
    Cherel, Ghislaine
    Blouin, Veronique
    Christophe, Olivier
    Moullier, Philippe
    Mingozzi, Federico
    VandenDriessche, Thierry
    MOLECULAR THERAPY, 2014, 22 (09) : 1605 - 1613
  • [40] Depletional Induction Therapy in Non-Human Primates - Preclinical Modeling of Polyclonal Depletion with Rhesus-Specific ATG.
    Schmitz, R.
    Mulvihill, M. S.
    Schroder, P. M.
    Fitch, Z.
    Leopardi, F.
    Magnani, D.
    Kwun, J.
    Knechtle, S. J.
    Kirk, A. D.
    AMERICAN JOURNAL OF TRANSPLANTATION, 2019, 19 : 597 - 597
12345