Genome Editing in Human Haematopoietic Stem Cells for the Treatment of X-Linked Agammaglobulinemia

被引：0
|
作者：
Bahal, Sameer [1 ]
Zinicola, Marta [1 ]
Vetharoy, Winston [1 ]
Whittaker, Thomas [1 ]
Naseem, Asma [1 ]
Blanco, Elena [1 ]
Rai, Rajeev [1 ]
Turchiano, Giandomenico [1 ]
Cavazza, Alessia [1 ,2 ]
Thrasher, Adrian J. [1 ,2 ]
Santilli, Giorgia [1 ,2 ]
机构：
[1] UCL, Mol & Cellular Immunol Sect, UCL Great Ormond St Inst Child Hlth, London, England
[2] NIHR Great Ormond St Hosp, Biomed Res Ctr, London, England
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
966
引用
收藏
页码：454 / 454
页数：1
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