Development of a novel AAV capsid with improved PNS tropism for treating Pompe disease by intravenous administration

被引：0
|
作者：
Kevany, B. M. [1 ]
Padegimas, L. [1 ]
Miller, T. J. [1 ]
机构：
[1] Abeona Therapeut Inc, Dallas, TX USA
来源：
HUMAN GENE THERAPY | 2019年 / 30卷 / 11期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P007
引用
收藏
页码：A21 / A21
页数：1
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