Novel Genome Editing Therapy Improves Disease Phenotype and Survival of a Mouse Model of Methylmalonic Acidemia

被引：0

作者：

Bastille, Amy ^{[1
]}

Zhang, Xiaohan ^{[1
]}

Ramesh, Nikhil ^{[1
]}

Vora, Jenisha ^{[1
]}

McCarthy, Elizabeth ^{[1
]}

Frank, Dylan ^{[1
]}

Ko, Chih-Wei ^{[1
]}

Wu, Carmen ^{[1
]}

Walsh, Noel ^{[1
]}

Liao, Jing ^{[1
]}

Gordo, Susana ^{[1
]}

Drouin, Lauren ^{[1
]}

Hebben, Matthias ^{[1
]}

Chiang, Kyle ^{[1
]}

Chau, Nelson ^{[1
]}

Zhang, Shengwen ^{[1
]}

机构：

[1] LogicBio Therapeut, Lexington, MA USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

324

引用

页码：160 / 161

页数：2

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