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机构:
Telethon Inst Genet & Med TIGEM, Pozzuoli, Italy
Univ Naples Federico II, Med Genet, Dept Translat Med, Naples, Italy
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Texas Childrens Hosp, Jan & Dan Duncan Neurol Res Inst, Houston, TX 77030 USA Rutgers State Univ, Dept Biol Sci, Newark, NJ USA