A novel AAV-based miQURE gene therapy for SCA3

被引：0
|
作者：
Toonen, L. J. A. [1 ]
Nobre, R. [2 ]
Haas, E. [3 ]
Huebener-Schmid, J. [3 ]
Martier, R. [1 ]
Valles, A. [1 ]
Higgens, J. J. [1 ]
van Deventer, S. [1 ]
Nguyen, H. P. [3 ]
Pereira de Almeida, L. [2 ]
Konstantinova, P. [1 ]
Evers, M. M. [1 ]
机构：
[1] UniQure Biopharma BV, Amsterdam, Netherlands
[2] Univ Coimbra, Coimbra, Portugal
[3] Inst Med Genet & Appl Genom, Tubingen, Germany
来源：
HUMAN GENE THERAPY | 2019年 / 30卷 / 11期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P247
引用
收藏
页码：A91 / A92
页数：2
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