Permanent phenotypic correction of Haemophilia B in immunocompetent mice by prenatal gene therapy

被引:0
|
作者
Waddington, SN
Nivsarkar, M
Mistry, A
Buckley, SMK
Kemball-Cook, G
Mosley, KL
Mitrophanous, K
Radcliffe, P
Holder, M
Brittan, M
Georgiadis, T
Al-Allaf, F
Bigger, B
Gregory, L
Cook, HT
Ali, RR
Thrasher, A
Tuddenham, EGD
Themis, M
Coutelle, C
机构
[1] Univ London Imperial Coll Sci Technol & Med, Gene Therapy Res Grp, Sect Cell & Mol Biol, London SW7 2AZ, England
[2] Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England
[3] Univ London Imperial Coll Sci Technol & Med, MRC, Ctr Clin Sci, London W12 0NN, England
[4] Univ London Imperial Coll Sci Technol & Med, Fac Med, Renal Med Sect, London W12 0NN, England
[5] Oxford BioMed UK Ltd, Oxford OX4 4GA, England
[6] Canc Res UK, Histopathol Unit, London WC2A 3PX, England
[7] UCL, Inst Ophthalmol, Dept Mol Genet, London EC1V 9EL, England
来源
JOURNAL OF GENE MEDICINE | 2004年 / 6卷 / 09期
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
42
引用
收藏
页码:S17 / S17
页数:1
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