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机构:
Jichi Med Univ, Ctr Open Innovat, Div Neurol Gene Therapy, 3311-1 Yakushiji, Shimotsuke, Tochigi 3290498, Japan
Univ Tokyo, Ctr Gene & Cell Therapy, Inst Med Sci, Minato Ku, 4-6-1 Shirokanedai, Tokyo 1080071, Japan Natl Taiwan Univ Hosp, Dept Med Genet & Pediat, 7 Chung Shan S Rd, Taipei, Taiwan