Long-Term Efficacy and Safety of the Microsomal Triglyceride Transfer Protein Inhibitor Lomitapide in Patients With Homozygous Familial Hypercholesterolemia

被引：104

作者：

Blom, Dirk J. ^{[1
]}

Averna, Maurizio R. ^{[2
]}

Meagher, Emma A. ^{[3
]}

Theron, Hendrik du Toit ^{[4
]}

Sirtori, Cesare R.

Hegele, Robert A. ^{[5
,6
]}

Shah, Prediman K. ^{[7
]}

Gaudet, Daniel ^{[8
]}

Stefanutti, Claudia ^{[9
]}

Vigna, Giovanni B. ^{[10
]}

Larrey, Dominique ^{[11
]}

Bloedon, LeAnne T. ^{[12
]}

Foulds, Pamela ^{[12
]}

Rader, Daniel J. ^{[3
]}

Cuchel, Marina ^{[3
]}

机构：

[1] Univ Cape Town, Cape Town, South Africa

[2] Univ Palermo, Palermo, Italy

[3] Univ Penn, Philadelphia, PA 19104 USA

[4] Netcare Private Hosp, Bloemfontein, South Africa

[5] Osped Niguarda Ca Granda, Milan, Italy

[6] Univ Western Ontario, London, ON, Canada

[7] Cedars Sinai Heart Inst, Los Angeles, CA USA

[8] Univ Montreal, Chicoutimi, PQ, Canada

[9] Univ Roma Sapienza, Rome, Italy

[10] Univ Ferrara, Ferrara, Italy

[11] CHRU Montpellier, Montpellier, France

[12] Aeger Pharmaceut, Cambridge, MA USA

来源：

CIRCULATION | 2017年 / 136卷 / 03期

关键词：

lomitapide;

D O I：

10.1161/CIRCULATIONAHA.117.028208

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：332 / 335

页数：4

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