CLINICAL OUTCOME STUDY FOR DYSFERLINOPATHY: THREE YEARS OF NATURAL HISTORY DATA FOR CLINICAL TRIAL READINESS

被引：0
|
作者：
James, M. K. [1 ]
Mayhew, A. G. [1 ]
Jacobs, M. [2 ,3 ]
Eagle, M.
Maron, E. [4 ]
Gee, R. [5 ]
Harman, M. [6 ]
Duong, T. [7 ]
Vandervelde, B. [8 ]
Siener, C. [9 ]
Thiele, S. [10 ]
Mendez, B. [11 ]
Canal, A. [12 ]
Sakamoto, C. [13 ]
Holsten, S. [14 ]
Pedrosa Belmonte, I. [15 ]
Semplicini, C. [16 ]
Alfano, L. [17 ]
Lowes, L. [17 ]
Straub, V. [1 ]
机构：
[1] John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England
[2] Childrens Natl Hlth Syst, Ctr Translat Sci, Div Biostat & Study Methodol, Washington, DC USA
[3] George Washington Univ, Pediat Epidemiol & Biostat, Washington, DC USA
[4] Elan Physio, Berlin, Germany
[5] Stanford Univ, Sch Med, Dept Neurol & Neurol Sci, Stanford, CA 94305 USA
[6] Childrens Hosp Westmead, Inst Neurosci & Muscle Res, Sydney, NSW, Australia
[7] Childrens Natl Hlth Syst, Dept Neurol, Washington, DC USA
[8] Aix Marseille Univ, La Timone Hosp, Neuromuscular & ALS Ctr, Marseille, France
[9] Washington Univ, Sch Med, Dept Neurol, St Louis, MO USA
[10] Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany
[11] Hosp Univ Virgen Rocio, Inst Biomed Sevilla, Dept Neurol, Neuromuscular Unit, Seville, Spain
[12] AP HP, Inst Myol, GH Pitie Salpe Triere 47-83,Blvd Hop, Paris, France
[13] Natl Ctr Neurol & Psychiat Tokyo, Natl Ctr Hosp, Dept Neurol, Tokyo, Japan
[14] Carolinas Healthcare Syst Neurosci Inst, Charlotte, NC USA
[15] Hosp Santa Creu & Sant Pau, Neurol Dept, Neuromuscular Disorders Unit, Barcelona, Spain
[16] Univ Padua, Dept Neurosci, Padua, Italy
[17] Nationwide Childrens Hosp, Columbus, OH USA
来源：
MUSCLE & NERVE | 2018年 / 58卷
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D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
7
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收藏
页码：S3 / S3
页数：1
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