Substrate reduction therapy approach for Sanfilippo C syndrome: use of iPSC and iPSC-derived neurons from patients as cellular models

被引：0
|
作者：
Beneto, N. [1 ]
Creus-Bachiller, E. [1 ]
Garcia-Morant, M. [1 ]
Grinberg, D. [1 ]
Vilageliu, L. [1 ]
Canals, I. [1 ,2 ]
机构：
[1] Univ Barcelona, Dept Genet Microbiol & Stat, Fac Biol, CIBERER,IBUB,IRSJD, Barcelona, Spain
[2] Univ Hosp, Lund Stem Cell Ctr, Stem Cells Aging & Neurodegenerat Grp, Lund, Sweden
来源：
EUROPEAN JOURNAL OF HUMAN GENETICS | 2019年 / 27卷
关键词：
D O I：
暂无
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
P06.64D
引用
收藏
页码：859 / 859
页数：1
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