Safety and long-term efficacy of AAV2-BEST1 gene augmentation therapy in canine model of Best vitelliform macular dystrophies

被引：0
|
作者：
Guziewicz, Karina E. [1 ]
Cideciyan, Artur V. [2 ]
Kendrick, Brian T. [1 ]
Dufour, Valerie L. [1 ]
Ruthel, Gordon [3 ]
Komaromy, Andras M. [4 ]
Iwabe, Simone [1 ]
Hauswirth, William [5 ]
Beltran, William A. [1 ]
Jacobson, Samuel G. [2 ]
Aguirre, Gustavo D. [1 ]
机构：
[1] Univ Penn, Clin Sci & Adv Med, Philadelphia, PA 19104 USA
[2] Univ Penn, Dept Ophthalmol, Philadelphia, PA 19104 USA
[3] Univ Penn, Dept Pathobiol, Philadelphia, PA 19104 USA
[4] Michigan State Univ, Dept Small Anim Clin Sci, E Lansing, MI 48824 USA
[5] Univ Florida, Dept Ophthalmol, Gainesville, FL 32611 USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2019年 / 60卷 / 09期
关键词：
D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
5200
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页数：3
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