Gene Augmentation Therapy in a Large Animal Model of PDE6A-Retinitis Pigmentosa Rescues Rod Function and Promotes Cone Survival Long-Term

被引：0
|
作者：
Occelli, Laurence M. [1 ]
Michalakis, Stylianos [2 ]
Schoen, Christian [2 ]
Biel, Martin [2 ]
Petersen-Jones, Simon M. [1 ]
机构：
[1] VMC Michigan State Univ, E Lansing, MI USA
[2] LMU, CIPSM Dept Pharm, Ctr Drug Res, Munich, Germany
来源：
MOLECULAR THERAPY | 2018年 / 26卷 / 05期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
367
引用
收藏
页码：171 / 172
页数：2
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