An AAV-CRISPR/Cas9 gene editing approach for GUCY2D-associated cone rod dystrophy (CORD6)

被引:0
|
作者
Mccullough, Kevin [1 ]
Boye, Sanford L. [1 ]
Fajardo, Diego [1 ]
Strang, Christianne E. [2 ]
Witherspoon, Douglas C. [2 ]
Gloskowski, Sebastian [3 ]
Dass, Abhishek [3 ]
Gamlin, Paul D. [2 ]
Maeder, Morgan [3 ]
Boye, Shannon Elizabeth [1 ]
机构
[1] Univ Florida, Ophthalmol, Gainesville, FL USA
[2] Univ Alabama Birmingham, Birmingham, AL USA
[3] Editas Med Inc, Cambridge, MA USA
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R77 [眼科学];
学科分类号
100212 ;
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6020
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页数:3
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