A Novel AAV-Based Gene Therapy for Spinal Muscular Atrophy

被引：0
|
作者：
Wu, Zhenhua [1 ]
Zhu, Peixin [1 ]
Wang, Qingzeng [1 ]
Li, Zhongwan [1 ]
Chen, Shuyuan [1 ]
Dai, Li [1 ]
Li, Junhui [1 ]
Wang, Lijun [1 ]
Ye, Guojie [1 ]
机构：
[1] Exegenesis Bio Inc, Spring House, PA USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
541
引用
收藏
页码：257 / 257
页数：1
相关论文
共 50 条
  • [1] A novel AAV-based gene therapy for glaucoma
    Wu, Ling
    Maturana, Carola
    Yao, Zuliang
    Wang, Wei
    Liang, Bo
    Hong, Laura
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2024, 65 (07)
  • [2] AAV9 Vector: a Novel modality in gene therapy for spinal muscular atrophy
    Rithu Pattali
    Yongchao Mou
    Xue-Jun Li
    Gene Therapy, 2019, 26 : 287 - 295
  • [3] AAV9 Vector: a Novel modality in gene therapy for spinal muscular atrophy
    Pattali, Rithu
    Mou, Yongchao
    Li, Xue-Jun
    GENE THERAPY, 2019, 26 (7-8) : 287 - 295
  • [4] AAV-based gene therapies for the muscular dystrophies
    Crudele, Julie M.
    Chamberlain, Jeffrey S.
    HUMAN MOLECULAR GENETICS, 2019, 28 (R1) : R102 - R107
  • [5] Next-Generation of AAV Gene Therapy for Spinal Muscular Atrophy
    Song, Chunjuan
    Wang, Qingzeng
    Lu, Qian
    Li, Zhongwan
    Lin, Zhucheng
    Zhou, Ying
    Chen, Shuyuan
    Wang, Lijun
    Ye, Guo-Jie
    Wu, Zhenhua
    MOLECULAR THERAPY, 2023, 31 (04) : 491 - 491
  • [6] Systemic AAV9 Gene Therapy of Spinal Muscular Atrophy
    Barkats, M.
    Benkhelifa-Ziyyat, S.
    Marais, T.
    Dominguez, E.
    Duque, S.
    Roda, M.
    Astord, S.
    Carcenac, R.
    Voit, T.
    HUMAN GENE THERAPY, 2011, 22 (10) : A16 - A17
  • [7] Development of Novel AAV-Based Gene Therapy for Cardiac Disease
    Whittlesey, K.
    Brooks, G.
    Szymanski, P.
    Beliakoff, G.
    Nye, J.
    Croze, R.
    Schmitt, C.
    Bickta, J.
    Barglow, K.
    Kotterman, M.
    Francis, P.
    Schaffer, D.
    Kirn, D.
    AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE, 2021, 203 (09)
  • [8] Adeno-associated virus (AAV) gene therapy for spinal muscular atrophy
    McMillan, Hugh
    JOURNAL OF THE NEUROLOGICAL SCIENCES, 2023, 455
  • [9] Optimization of AAV9-SMN gene therapy for Spinal Muscular Atrophy
    Besse, Aurore
    Marais, Thibaut
    Astord, Stephanie
    Roda, Marianne
    Tanguy, Yannick
    Clement, Yan
    Barkats, Martine
    HUMAN GENE THERAPY, 2014, 25 (11) : A102 - A103
  • [10] Gene therapy in spinal muscular atrophy
    Audic, Frederique
    ARCHIVES DE PEDIATRIE, 2023, 30 (08): : 8S12 - 8S17
12345