Updated results of Transpher A: multicenter, single-dose, phase 1/2 clinical trial of ABO-102 for Sanfilippo syndrome type A (mucopolysaccharidosis IIIA)

被引：0
|
作者：
Flanigan, Kevin [1 ]
Smith, Nicholas [2 ]
Couce, Maria [3 ]
Escolar, Maria [4 ]
Truxal, Kristen [1 ]
McBride, Kim [1 ]
de Castro, Maria [3 ]
Fuller, Maria [2 ]
Paneda, Astrid [5 ]
Ruiz, Juan [5 ]
机构：
[1] Nationwide Childrens Hosp, Columbus, OH USA
[2] Womens & Childrens Hosp, Adelaide, SA, Australia
[3] Hosp Clin Univ Santiago de Compostela, Santiago De Compostela, Spain
[4] Univ Pittsburgh, Med Ctr, Pittsburgh, PA 15260 USA
[5] Abeona Therapeut, Dallas, TX USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2021年 / 132卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
eP203
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收藏
页码：S133 / S134
页数：3
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