OUTCOMES OF GENE THERAPY FOR BETA-THALASSEMIA MAJOR VIA TRANSPLANTATION OF AUTOLOGOUS HEMATOPOIETIC STEM CELLS TRANSDUCED EX VIVO WITH A LENTIVIRAL BETA GLOBIN VECTOR.

被引：0
|
作者：
Cavazzana, M. [1 ]
Ribeil, J. A. [1 ]
Payen, E. [2 ,3 ]
Suarez, F. [4 ]
Negre, O. [5 ]
Beuzard, Y. [2 ,3 ]
Touzot, F. [1 ]
Cavallesco, R. [6 ,7 ]
Lefrere, F. [1 ]
Chretien, S. [2 ,3 ]
Bourget, P. [8 ]
Monpoux, F. [9 ]
Pondarre, C. [10 ]
Neven, B. [11 ]
Bushman, F. D. [12 ]
Schmidt, M. [13 ,14 ]
von Kalle, C. [13 ,14 ]
Sandler, L. [15 ]
Soni, S. [15 ]
Ryu, B. [15 ]
Kutner, R. [15 ]
Veres, G. [15 ]
Finer, M. [15 ]
Blanche, S. [11 ]
Hermine, O. [4 ]
Hacein-Bey-Abina, S. [1 ]
Leboulch, P. [2 ,3 ,6 ,7 ]
机构：
[1] Hop Univ Necker Enfants Malad, Dept Biotherapie, Paris, France
[2] Univ Paris 11, INSERM, CEA, UMR 962, Orsay, France
[3] CEA, Inst Emerging Dis & Innovat Therapies iMETI, Fontenay Aux Roses, France
[4] Hop Univ Necker Enfants Malad, Serv Hematol Adulte, Paris, France
[5] CEA, IMETI, Bluebird Bio France, Fontenay Aux Roses, France
[6] Harvard Univ, Sch Med, Boston, MA USA
[7] Brigham & Womens Hosp, Boston, MA 02115 USA
[8] Hop Univ Necker Enfants Malad, Clin Pharm Dept, Paris, France
[9] Ctr Hosp Nice Sophia Antipolis, Unite Hematooncol Infantile, Nice, France
[10] CHIC, Ctr Reference Drepanocytose, Serv Pediat, Creteil, France
[11] Hop Univ Necker Enfants Malad, Unite Immunol Hematol Pediat, Paris, France
[12] Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA
[13] Natl Ctr Tumor Dis NCT, Heidelberg, Germany
[14] German Canc Res Ctr, Heidelberg, Germany
[15] Bluebird Bio, Cambridge, England
来源：
HAEMATOLOGICA | 2014年 / 99卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
S742
引用
收藏
页码：268 / 268
页数：1
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