The Advent of Omics Sciences in Clinical Trials of Motor Neuron Diseases

被引:7
|
作者
Ruffo, Paola [1 ]
Cavallaro, Sebastiano [2 ]
Conforti, Francesca Luisa [1 ]
机构
[1] Univ Calabria, Dept Pharm Hlth & Nutr Sci, Med Genet Lab, I-87036 Arcavacata Di Rende, Italy
[2] Natl Res Council CNR, Inst Biomed Res & Innovat IRIB, I-95126 Catania, Italy
来源
JOURNAL OF PERSONALIZED MEDICINE | 2022年 / 12卷 / 05期
关键词
clinical trials; omics; personalized medicine; neurodegenerative disease; motor neuron disease; amyotrophic lateral sclerosis; spinal muscular atrophy; genomics; transcriptomics; AMYOTROPHIC-LATERAL-SCLEROSIS; SPINAL MUSCULAR-ATROPHY; ABEPARVOVEC GENE-THERAPY; OPEN-LABEL; ANTISENSE OLIGONUCLEOTIDE; SINGLE-ARM; MULTICENTER;
D O I
10.3390/jpm12050758
中图分类号
R19 [保健组织与事业(卫生事业管理)];
学科分类号
摘要
The "omics revolution" has totally changed the scientific research approach and is contributing to the development of personalized therapies. In motor neuron diseases (MNDs), a set of complex, multifactorial, late-onset and chronic neurodegenerative diseases, the use of multi-omics approaches in clinical trials is providing new opportunities to stratify patients and develop target therapies. To show how omics science is gaining momentum in MNDs, in this work, we review the interventional clinical trials for MNDs based on the application of omics sciences. We analyze a total of 62 clinical trials listed in the ClinicalTrials database where different omics approaches have been applied in an initial phase, for diagnosis or patient selection, or in subsequent stages to cluster subjects, identify molecular signatures or evaluate drugs security or efficacy. The rise of omics sciences in clinical experimentation of MNDs is leading to an upheaval in their diagnosis and therapy that will require significant investments and means to ensure the correct and rapid evolution of personalized medicine.
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页数:14
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