Long-term safety and efficacy of pegunigalsidase alfa: A multicenter extension study in adult patients with Fabry disease

被引：0

作者：

Hughes, Derralynn ^{[1
]}

Gonzalez, Derlis ^{[2
]}

Maegawa, Gustavo ^{[3
]}

Bernat, John ^{[4
]}

Holida, Myrl ^{[4
]}

Giraldo, Pilar ^{[5
]}

Atta, Mohamed ^{[6
]}

Chertkoff, Raul ^{[7
]}

Alon, Sari ^{[7
]}

Almon, Einat B. ^{[7
]}

Rocco, Rossana ^{[8
]}

Goker-Alpan, Ozlem ^{[9
]}

机构：

[1] UCL, London, England

[2] Inst Privado Hematol & Invest Clin, Asuncion, Paraguay

[3] Univ Florida, Gainesville, FL USA

[4] Univ Iowa Hlth Care, Iowa City, IA USA

[5] Hosp Dia Quiron, Zaragoza, Spain

[6] Johns Hopkins Sch Med, Baltimore, MD USA

[7] Protalix Biotherapeut, Carmiel, Israel

[8] Chiesi Farmaceut SpA, Parma, Italy

[9] Lysosomal Disorders Res & Treatment Unit, Fairfax, VA USA

来源：

MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2021.11.143

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

128

引用

页码：S58 / S58

页数：1

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