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- [21] Reduction of Atxn2, a Therapeutic Target for Sporadic ALS, in Non-Human Primates Using a Novel, Intravenously Delivered AAV CapsidMOLECULAR THERAPY, 2024, 32 (04) : 162 - 162Murlidharan, GiridharGrandell, EmilyJanack, StephenBerry, AmandaGuelin, IsabelleGualtieri, CharlesIronside, TylerScott, ElizabethPryce, CynthiaMastis, BryanSami, Ramin KamranEdwards, MattReece-Hoyes, JohnWest, CaraCalcedo, RobertoGoswami, DharmendraCao, SherryStanek, Lisa M.Lilley, GrahamRichman, Laura K.Albright, Charles F.
- [22] One-Time Intrathecal Administration of AAV5-miATXN3 in Non-Human PrimatesMOLECULAR THERAPY, 2020, 28 (04) : 215 - 216Evers, Melvin M.Toonen, LodewijkSpronck, LisaBrouwers, CynthiaMariet, FannyBaatje, SumiatiSchwarz, Lukasvan Deventer, SanderSier-Ferreira, Valeriede Haan, MartinValles, AstridKonstantinova, Pavlina
- [23] Optimizing MRI-Guided Intra-Striatal AAV Dose Administration in Non-Human PrimatesMOLECULAR THERAPY, 2022, 30 (04) : 128 - 128Bu, JieElmer, BradfordAssaf, BaselDangler, CharlesGoulet, MartinMueller, ChristianRamachandran, Shyam
- [24] Intravitreal injection of a rationally designed AAV capsid library in non-human primate identifies variants with enhanced retinal transduction and neutralizing antibody evasionMOLECULAR THERAPY, 2023, 31 (12) : 3441 - 3456Kellish, Patrick C.Marsic, DamienCrosson, Sean M.Choudhury, ShreyasiScalabrino, Miranda L.Strang, Christianne E.Hill, JulieMcCullough, K. TylerPeterson, James J.Fajardo, DiegoGupte, SiddhantMakal, VictoriaKondratov, OleksandrKondratova, LiudmylaIyer, SivaWitherspoon, C. DouglasGamlin, Paul D.Zolotukhin, SergeiBoye, Sanford L.Boye, Shannon E.
- [25] Efficient In Vivo Gene Editing of Inherited Retinal Disease Genes in Mice and Non-Human PrimatesMOLECULAR THERAPY, 2017, 25 (05) : 353 - 354Boye, ShannonStefanidakis, MichaelMepani, RinaSkor, Maxwell N.Gloskowski, Sebastian W.Horng, JoyMcCullough, Kevin T.Marco, EugenioGiannoukos, GeorgiaCiulla, DawnChao, HosonBounoutas, George S.Witherspoon, C. DouglasWilson, ChristopherBumcrot, DavidGamlin, PaulBoye, SanfordJiang, HaiyanAlbright, CharlieMaeder, Morgan L.
- [26] A Novel Liver-Tropic AAV Capsid sL65 Shows Superior Transduction and Efficacy in Humanized Mice and Non-Human PrimatesMOLECULAR THERAPY, 2021, 29 (04) : 11 - 12Liao, JingBastille, AmyDrouin, LaurenEdwards, MattFrank, DylanFreland, LaureGordo, SusanaKo, Chih-WeiMiller-Medzon, NoahMcCarthy, ElizabethRamesh, NikhilVillareal, ValerieVora, JenishaWu, CarmenWalsh, NoelXiong, JohnZhang, XiaohanZhang, ShengwenCreus, Marti CabanesLisowski, LeszekChau, NelsonChiang, KyleHebben, Matthias
- [27] STRV5, a Liver Detargeted AAV Capsid Demonstrates Improved Safety Profile After Intravenous Administration of High Doses in Non-Human PrimatesMOLECULAR THERAPY, 2022, 30 (04) : 339 - 339Gulledge, TravisAustin, BridgetBandoski-Gralinski, CherylAsokan, AravindRivera, Ruth Castellanos
- [28] Successful Repeated Hepatic Gene Delivery in Mice and Non-human Primates Achieved by Sequential Administration of AAV5ch and AAV1MOLECULAR THERAPY, 2017, 25 (08) : 1831 - 1842Majowicz, AnnaSalas, DavidZabaleta, NereaRodriguez-Garcia, EstefaniaGonzalez-Aseguinolaza, GloriaPetry, HaraldFerreira, Valerie
- [29] Efficient Retinal Transduction by AAV Variants Identified via Directed Evolution and Screening in Non-Human PrimateMOLECULAR THERAPY, 2020, 28 (04) : 257 - 258Boye, Shannon E.Choudhury, ShreyasiMarsic, DamienKondratov, OleksandrPotter, MarkPeterson, JamesCalabro, KaitlynStrang, ChristianneZolotukhin, SergeiGamlin, PaulBoye, Sanford
- [30] Expanding the AAV Toolbox for Cerebellar Transduction: Identifying and Characterizing Novel Variants in Non-Human Primates and MiceMOLECULAR THERAPY, 2021, 29 (04) : 27 - 27Keiser, Megan S.Chen, Yong HongRanum, Paul T.Liu, XueyuanCheng, CongshengLeib, DavidSmith, GearyMuehlmatt, AmyTecedor, LuisDavidson, Beverly L.