Characterization of a novel AAV capsid with enhanced brain transduction following systemic delivery

被引:0
|
作者
Glenn, J. D. [1 ]
Yost, S. [1 ]
Firnberg, E. [1 ]
Mercer, A. [1 ]
Liu, Y. [1 ]
Coruzzi, L. [1 ]
Danos, O. [1 ]
Bruder, J. T. [1 ]
Karumuthil-Melethil, S. [1 ]
机构
[1] ReGenX Biosci, Rockville, MD USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
P011
引用
收藏
页码:A22 / A22
页数:1
相关论文
共 50 条
  • [31] Enteric Nervous System Transduction Following IV Delivery of Multiple AAV Serotypes
    Lampe, Sara Gombash
    Cowley, Christopher
    Fitzgerald, Julie
    Mueller, Christian
    Christofi, Fedias
    Foust, Kevin
    FASEB JOURNAL, 2015, 29
  • [32] Enteric Nervous System Transduction Following Intravascular Delivery of AAV9
    Lampe, S. E. Gombash
    Cowley, C. J.
    Christofi, F. L.
    Fitzgerald, J. A.
    Foust, K. D.
    MOLECULAR THERAPY, 2014, 22 : S91 - S91
  • [33] Quantifying capsid peptide: MHC I complexes following adeno-associated virus (AAV) transduction
    Pien, G. C.
    Hasbrouck, N. C.
    Maus, M. V.
    Mingozzi, F.
    High, K. A.
    JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2008, 121 (02) : S173 - S173
  • [34] Differential Transduction Following Basal Ganglia Administration of Distinct Pseudotyped AAV Capsid Serotypes in Nonhuman Primates
    Dodiya, Hemraj B.
    Bjorklund, Tomas
    Stansell, James, III
    Mandel, Ronald J.
    Kirik, Deniz
    Kordower, Jeffrey H.
    MOLECULAR THERAPY, 2010, 18 (03) : 579 - 587
  • [35] CB 2679d-GT - A Novel Human Factor IX Variant Shows Enhanced Activity After Delivery Into Hemophilic Mice Using an AAV Capsid with High Liver Transduction
    Pekrun, Katja
    Blouse, Grant E.
    Zhang, Feijie
    Le Moan, Natacha
    Knudsen, Tom
    Landau, Jeff
    Kay, Mark A.
    MOLECULAR THERAPY, 2020, 28 (04) : 172 - 173
  • [36] Novel AAV Variants Isolated by Directed Evolution in Primate Display Enhanced Retinal Transduction Following Intravitreal Injection
    Boye, Sanford L.
    Choudhury, Shreyasi
    Marsic, Damien
    Strang, Christianne
    Peterson, James J.
    Fajardo, Diego
    Bennett, Antonette
    Agbandje-McKenna, Mavis
    Witherspoon, C. Douglas
    Gamlin, Paul D.
    Zolotukhin, Sergei
    Boye, Shannon E.
    MOLECULAR THERAPY, 2017, 25 (05) : 231 - 232
  • [37] Novel AAV variants isolated by directed evolution in primate display enhanced retinal transduction following intravitreal injection
    Choudhury, Shreyasi
    Marsic, Damien
    Peterson, James
    Fajardo, Diego
    Bennett, Antonette
    Gamlin, Paul D.
    Agbandje-McKenna, Mavis
    Zolotukhin, Sergei
    Boye, Sanford L.
    Boye, Shannon Elizabeth
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2017, 58 (08)
  • [38] A Novel AAV Capsid with a Potential of Crossing NHP Blood-Brain Barrier
    Li, Shaoyong
    Wang, Wei
    Lu, Xiaodong
    Wang, Hongxing
    Huang, Carol
    Tocci, Jenna
    Ren, Xiaoqin
    Ren, Amy
    Shang, Jianyu
    Zhou, Pengcheng
    Hefferan, Michael
    Nonnenmacher, Mathieu
    Cabral, Joseph
    Hou, Jay
    MOLECULAR THERAPY, 2020, 28 (04) : 253 - 253
  • [39] In Vitro Characterization of Novel AAV-Spark100 and AAV-Spark200 Capsid Variants
    Yazicioglu, Mustafa N.
    Armour, Sean M.
    Keiser, Nicholas W.
    Mingozzi, Federico
    Anguela, Xavier M.
    MOLECULAR THERAPY, 2018, 26 (05) : 47 - 48
  • [40] Immunobiology of a rationally-designed AAV2 capsid following intravitreal delivery in mice
    Whitehead, Michael
    Sage, Andrew
    Burgoyne, Tom
    Osborne, Andrew
    Yu-Wai-Man, Patrick
    Martin, Keith R.
    GENE THERAPY, 2023, 30 (09) : 723 - 735