Clinical benefits of miglustat on bone disease in adult type 1 Gaucher disease (GD1): A meta-analysis

被引：0
|
作者：
Pastores, G. M.
Elstein, D.
Hrebicek, M.
Zimran, A.
机构：
[1] NYU, Sch Med, Dept Neurol & Pediat, New York, NY USA
[2] Shaare Zedek Med Ctr, Dept Med, IL-91000 Jerusalem, Israel
[3] Inst IMD, Prague, Czech Republic
来源：
CALCIFIED TISSUE INTERNATIONAL | 2007年 / 80卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：S68 / S68
页数：1
相关论文
共 50 条
  • [41] Substrate reduction therapy: miglustat as a remedy for symptomatic patients with Gaucher disease type 1
    Pastores, GM
    Barnett, NL
    EXPERT OPINION ON INVESTIGATIONAL DRUGS, 2003, 12 (02) : 273 - 281
  • [42] Clinical Manifestations of Type 1 Gaucher Disease
    Salehpour, Shadab
    IRANIAN JOURNAL OF CHILD NEUROLOGY, 2012, 6 (04) : 13 - 14
  • [43] A CLINICAL STUDY TO ASSESS MIGLUSTAT AS MAINTENANCE THERAPY FOR ADULT PATIENTS WITH STABLE TYPE 1 GAUCHER DISEASE (GD 1) AFTER SWITCH FROM ENZYME REPLACEMENT THERAPY (ERT): OBJECTIVES AND STUDY DESIGN
    Ait-Aissa, N.
    Jamieson, V
    Morand, O.
    Esparza, I
    Goffin, H.
    JOURNAL OF INHERITED METABOLIC DISEASE, 2005, 28 : 170 - 170
  • [44] Changes in the atherogenic profile of patients with type 1 Gaucher disease after miglustat therapy
    Puzo, J.
    Alfonso, P.
    Irun, P.
    Gervas, J.
    Pocovi, M.
    Giraldo, P.
    ATHEROSCLEROSIS, 2010, 209 (02) : 515 - 519
  • [45] Successful switch from enzyme replacement therapy to miglustat in an adult patient with type 1 Gaucher disease: a case report
    Giuffrida G.
    Lombardo R.
    Di Francesco E.
    Parrinello L.
    Di Raimondo F.
    Fiumara A.
    Journal of Medical Case Reports, 10 (1) : 1 - 6
  • [46] A Comprehensive Study of Bone Manifestations in Adult Gaucher Disease Type 1 Patients in Argentina
    Beatriz Oliveri
    Diana González
    Felisa Quiroga
    Claudio Silva
    Paula Rozenfeld
    Calcified Tissue International, 2019, 104 : 650 - 657
  • [47] A Comprehensive Study of Bone Manifestations in Adult Gaucher Disease Type 1 Patients in Argentina
    Oliveri, Beatriz
    Gonzalez, Diana
    Quiroga, Felisa
    Silva, Claudio
    Rozenfeld, Paula
    CALCIFIED TISSUE INTERNATIONAL, 2019, 104 (06) : 650 - 657
  • [48] Short-term effect of oral treatment with miglustat in type 1 Gaucher disease.
    Giraldo, P
    Alonso, D
    Acedo, M
    Franco, R
    Barez, A
    Corrales, A
    Serrano, D
    Roldan, V
    Latre, P
    Alfonso, P
    Pocovi, M
    BLOOD, 2005, 106 (11) : 629A - 630A
  • [49] Twelve years of experience with miglustat in the treatment of type 1 Gaucher disease: The Spanish ZAGAL project
    Giraldo, Pilar
    Andrade-Campos, Marcio
    Alfonso, Pilar
    Irun, Pilar
    Atutxa, Koldo
    Acedo, Antonio
    Barez, Abelardo
    Blanes, Margarita
    Diaz-Morant, Vicente
    Angeles Fernandez-Galan, Ma
    Franco, Rafael
    Gil-Cortes, Cristina
    Giner, Vicente
    Ibanez, Angela
    Latre, Paz
    Loyola, Ines
    Luno, Elisa
    Hernandez-Martin, Roberto
    Medrano-Engay, Blanca
    Puerta, Jose
    Roig, Inmaculada
    de la Serna, Javier
    Salamero, Olga
    Villalon, Lucia
    Pocovi, Miguel
    BLOOD CELLS MOLECULES AND DISEASES, 2018, 68 : 173 - 179
  • [50] TEN YEARS OF EXPERIENCE WITH MIGLUSTAT IN TREATMENT OF TYPE 1 GAUCHER DISEASE: THE SPANISH ZAGAL PROJECT
    Giraldo, P.
    Andrade, M.
    Alfonso, P.
    Irun, P.
    Atucha, L.
    Acedo, A.
    Diaz-Morant, V.
    Barez, A.
    Fernandez-Galan, M.
    Franco, R.
    Giner, V.
    Loyola, I.
    Luno, E.
    de la Serna, J.
    Villalon, L.
    Salamero, O.
    Pocovi, M.
    HAEMATOLOGICA, 2014, 99 : 764 - 764
12345