Antisense oligonucleotide therapy for TTR amyloidosis

被引:0
|
作者
Benson, M. D. [1 ,2 ]
Pandey, S. [3 ]
Witchell, D. [3 ]
Jazayeri, A. [3 ]
Siwkowski, A. [3 ]
Monia, B. [3 ]
Kluve-Beckerman, B. [1 ]
机构
[1] Indiana Univ Sch Med, Dept Pathol & Lab Med, Indianapolis, IN USA
[2] Richard L Roudebush Vet Affairs Med Ctr, Indianapolis, IN 46202 USA
[3] ISIS Pharmaceut, Carlsbad, CA 92008 USA
关键词
D O I
暂无
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
引用
收藏
页码:53 / 53
页数:1
相关论文
共 50 条
  • [21] Antisense oligonucleotide therapy for neurodegenerative disease
    Smith, Richard A.
    Miller, Timothy M.
    Yamanaka, Koji
    Monia, Brett P.
    Condon, Thomas F.
    Hung, Gene
    Lobsiger, Christian S.
    Ward, Chris M.
    McAlonis-Downes, Melissa
    Wei, Hongbing
    Wancewicz, Ed V.
    Bennett, C. Frank
    Cleveland, Don W.
    JOURNAL OF CLINICAL INVESTIGATION, 2006, 116 (08): : 2290 - 2296
  • [22] Antisense Oligonucleotide Therapy for Lafora Disease
    Ahonen, Saija
    Grossman, Tamar
    Turnbull, Julie
    Kordasiewicz, Holly
    Katz, Melanie
    McCaleb, Michael
    Wang, Peixiang
    Zhao, Xiaochu
    Minassian, Berge
    NEUROLOGY, 2018, 90
  • [23] Treatment of transthyretin cardiomyopathy with a TTR-specific antisense oligonucleotide (IONIS-TTRRx)
    Benson, Merrill D.
    Ackermann, Elizabeth J.
    Monia, Brett P.
    AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2017, 24 : 134 - 135
  • [24] siRNA therapy for TTR-related ocular amyloidosis
    Tasaki, M.
    Jono, H.
    Ueda, M.
    Hara, R.
    Obayashi, K.
    Kawaji, T.
    Rene, A.
    Mori, Y.
    Yamashita, T.
    Ando, Y.
    AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2010, 17 : 52 - 53
  • [25] Inotersen (transthyretin-specific antisense oligonucleotide) for treatment of transthyretin amyloidosis
    Benson, Merrill D.
    Dasgupta, Noel R.
    Monia, Brett P.
    NEURODEGENERATIVE DISEASE MANAGEMENT, 2019, 9 (01) : 25 - 30
  • [26] Peptide-oligonucleotide hybrids in antisense therapy
    Pierce, TL
    White, AR
    Tregear, GW
    Sexton, PM
    MINI-REVIEWS IN MEDICINAL CHEMISTRY, 2005, 5 (01) : 41 - 55
  • [27] Carbohydrate modifications in antisense oligonucleotide therapy.
    Manoharan, M
    ABSTRACTS OF PAPERS OF THE AMERICAN CHEMICAL SOCIETY, 2000, 219 : U245 - U246
  • [28] Antisense oligonucleotide exon skipping therapy for DMD
    Wood, M. J. A.
    NEUROMUSCULAR DISORDERS, 2011, 21 (9-10) : 702 - 702
  • [29] Antisense Oligonucleotide Therapy for Inherited Retinal Dystrophies
    Gerard, Xavier
    Garanto, Alejandro
    Rozet, Jean-Michel
    Collin, Rob W. J.
    RETINAL DEGENERATIVE DISEASES: MECHANISMS AND EXPERIMENTAL THERAPY, 2016, 854 : 517 - 524
  • [30] Restoring splicing defects by antisense oligonucleotide therapy
    Collin, R. W.
    EUROPEAN JOURNAL OF HUMAN GENETICS, 2019, 27 : 1050 - 1051