Genetic correction of induced pluripotent stem cells from a Wiskott-Aldrich Syndrome patient normalizes the immune defects

被引：0
|
作者：
Davis, Brian R. [1 ]
Laskowski, Tamara J. [1 ]
Van Caeneghem, Yasmine [2 ]
Pourebrahim, Rasoul [1 ]
Li, Xuan Shirley [1 ]
Liao, Wei [1 ]
Garate, Zita [1 ,3 ]
Crane, Ana [1 ]
Carlos Segovia, Jose [3 ]
Holmes, Michael [4 ]
Ni, Zhenya [5 ,6 ]
Kaufman, Dan [5 ,6 ]
Vandekerckhove, Bart [2 ]
机构：
[1] Univ Texas Hlth Sci Ctr Houston, Inst Mol Med, Ctr Stem Cell & Regenerat Med, Houston, TX 77030 USA
[2] Univ Ghent, Expt Immunol Lab, B-9000 Ghent, Belgium
[3] Ctr Invest Energet Medioambientales & Tecnol, Hematopoiesis & Gene Therapy Div, Differentiat & Cytometry Unit, Madrid 28040, Spain
[4] Sangamo BioSci, Richmond, CA 94804 USA
[5] Univ Minnesota, Dept Med, Minneapolis, MN 55455 USA
[6] Univ Minnesota, Stem Cell Inst, Minneapolis, MN 55455 USA
来源：
HUMAN GENE THERAPY | 2014年 / 25卷 / 11期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
OR047
引用
收藏
页码：A40 / A40
页数：1
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