Genetic correction of induced pluripotent stem cells from a Wiskott-Aldrich Syndrome patient normalizes the immune defects

被引：0

作者：

Davis, Brian R. ^{[1
]}

Laskowski, Tamara J. ^{[1
]}

Van Caeneghem, Yasmine ^{[2
]}

Pourebrahim, Rasoul ^{[1
]}

Li, Xuan Shirley ^{[1
]}

Liao, Wei ^{[1
]}

Garate, Zita ^{[1
,3
]}

Crane, Ana ^{[1
]}

Carlos Segovia, Jose ^{[3
]}

Holmes, Michael ^{[4
]}

Ni, Zhenya ^{[5
,6
]}

Kaufman, Dan ^{[5
,6
]}

Vandekerckhove, Bart ^{[2
]}

机构：

[1] Univ Texas Hlth Sci Ctr Houston, Inst Mol Med, Ctr Stem Cell & Regenerat Med, Houston, TX 77030 USA

[2] Univ Ghent, Expt Immunol Lab, B-9000 Ghent, Belgium

[3] Ctr Invest Energet Medioambientales & Tecnol, Hematopoiesis & Gene Therapy Div, Differentiat & Cytometry Unit, Madrid 28040, Spain

[4] Sangamo BioSci, Richmond, CA 94804 USA

[5] Univ Minnesota, Dept Med, Minneapolis, MN 55455 USA

[6] Univ Minnesota, Stem Cell Inst, Minneapolis, MN 55455 USA

来源：

HUMAN GENE THERAPY | 2014年 / 25卷 / 11期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

OR047

引用

页码：A40 / A40

页数：1

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