Fetal Gene Therapy for Acute Neuronopathic Gaucher Disease

被引：0

作者：

Rahim, Ahad A. ^{[1
]}

Wong, Andrew M. ^{[2
]}

Buckley, Suzanne M. ^{[1
]}

Hughes, Derralynn A. ^{[1
]}

Karlsson, Stefan ^{[3
]}

Cooper, Jonathan D. ^{[2
]}

Thrasher, Adrian J. ^{[4
]}

Mehta, Atul ^{[1
]}

Waddington, Simon N. ^{[1
]}

机构：

[1] UCL, Sch Med, Dept Haematol, London W1N 8AA, England

[2] Kings Coll London, Dept Neurosci, London WC2R 2LS, England

[3] Lund Univ, Lund, Sweden

[4] UCL, Inst Child Hlth, Mol Immunol Unit, London, England

来源：

MOLECULAR THERAPY | 2009年 / 17卷

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：S357 / S357

页数：1

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