Fetal Gene Therapy for Acute Neuronopathic Gaucher Disease

被引：0
|
作者：
Rahim, Ahad A. [1 ]
Wong, Andrew M. [2 ]
Buckley, Suzanne M. [1 ]
Hughes, Derralynn A. [1 ]
Karlsson, Stefan [3 ]
Cooper, Jonathan D. [2 ]
Thrasher, Adrian J. [4 ]
Mehta, Atul [1 ]
Waddington, Simon N. [1 ]
机构：
[1] UCL, Sch Med, Dept Haematol, London W1N 8AA, England
[2] Kings Coll London, Dept Neurosci, London WC2R 2LS, England
[3] Lund Univ, Lund, Sweden
[4] UCL, Inst Child Hlth, Mol Immunol Unit, London, England
来源：
MOLECULAR THERAPY | 2009年 / 17卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
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页码：S357 / S357
页数：1
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