Gene Editing for Congenital Dyserythropoietic Anemia Type II Model in Human Hematopoietic Stem and Progenitor Cells

被引：0

作者：

Dessy-Rodriguez, Mercedes ^{[1
,2
]}

Fananas-Baquero, Sara ^{[1
,2
]}

Venturi, Veronica ^{[3
]}

Payan, Salvador ^{[4
]}

Tornador, Cristian ^{[5
]}

Hernandez, Gonzalo ^{[6
]}

Sanchez Fernandez, Mayka ^{[5
,6
]}

Bueren, Juan A. ^{[1
,2
]}

Carlos Segovia, Jose ^{[1
,2
]}

Quintana-Bustamante, Oscar ^{[1
,2
]}

机构：

[1] CIEMAT CIBERER, Biomed Innovat Unit, Madrid, Spain

[2] IIS FJD, Unidad Mixta Terapias Avanzadas, Madrid, Spain

[3] Univ Int Catalunya, Madrid, Spain

[4] Hosp Univ Virgen del Rocio, Seville, Spain

[5] Bloodgenetics, Barcelona, Spain

[6] Univ Int Catalunya, Barcelona, Spain

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

701

引用

页码：341 / 341

页数：1

共 50 条

[31] UPDATE ON THE EUROPEAN CONSORTIUM FOR CONGENITAL DYSERYTHROPOIETIC ANEMIA TYPE II
A Iolascon
J Delaunay
S Wickramaisinghe
H Heimpel
S Perrotta
E Miraglia Del Giudice
R Carbone
Pediatric Research, 1999, 45 : 943 - 943
[32] A FAMILY WITH CONGENITAL DYSERYTHROPOIETIC ANEMIA TYPE-II (HEMPAS)
OMINE, M
YAMAUCHI, H
NOGIWA, E
UMEGAE, S
TSUCHIYA, J
MAEKAWA, T
ACTA HAEMATOLOGICA JAPONICA, 1981, 44 (01): : 1 - 15
[33] A novel variant mutation for congenital dyserythropoietic anemia, type II
Song, Joo Y.
Pawar, Anjali
Collins, Christin
BLOOD CELLS MOLECULES AND DISEASES, 2014, 53 (04) : 272 - 273
[34] CEREBRAL STROKE IN A CHILD WITH CONGENITAL DYSERYTHROPOIETIC ANEMIA TYPE II
Ozcan, A.
Patiroglu, T.
Acer, H.
Gumus, H.
Senol, S.
Karakukcu, M.
Ozdemir, M. A.
Unal, E.
HAEMATOLOGICA, 2016, 101 : 872 - 873
[35] Piebaldism associated with congenital dyserythropoietic anemia type II (HEMPAS)
Köklü, S
Ertugrul, D
Onat, AM
Karakus, S
Haznedaroglu, IC
Büyükasik, Y
Sayinalp, N
Özcebe, O
Dündar, SV
AMERICAN JOURNAL OF HEMATOLOGY, 2002, 69 (03) : 210 - 213
[36] A CASE OF CONGENITAL DYSERYTHROPOIETIC ANEMIA TYPE-II (HEMPAS)
MORIWAKI, Y
MATSUI, K
FUJIOKA, H
IWAHASHI, N
SENO, T
TAMURA, S
YAMAMOTO, T
AMURO, Y
HADA, T
HIGASHINO, K
ACTA HAEMATOLOGICA JAPONICA, 1985, 48 (01): : 29 - 36
[37] Update on the European Consortium for congenital dyserythropoietic anemia type II
Iolascon, A
Delaunay, J
Wickramaisinghe, S
Heimpel, H
Perrotta, S
del Giudice, EM
Carbone, R
PEDIATRIC RESEARCH, 1999, 45 (06) : 943 - 943
[38] Interferon therapy in congenital dyserythropoietic anemia type I/II
Marwaha, RK
Bansal, D
Trehan, A
Garewal, G
PEDIATRIC HEMATOLOGY AND ONCOLOGY, 2005, 22 (02) : 133 - 138
[39] GAUCHER-LIKE CELLS AND CONGENITAL DYSERYTHROPOIETIC ANEMIA, TYPE-II (HEMPAS)
VANDORPE, A
ORSHOVEN, AB
DESMET, V
VERWILGHEN, RL
BRITISH JOURNAL OF HAEMATOLOGY, 1973, 25 (02) : 165 - +
[40] CONGENITAL DYSERYTHROPOIETIC ANEMIA TYPE-II - PERSONAL OBSERVATION
GANDULLIA, E
VENEZIANO, G
MINERVA PEDIATRICA, 1981, 33 (09) : 423 - 428

← 1 2 3 4 5 →