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- [21] Nusinersen treatment and cerebrospinal fluid neurofilaments: An explorative study on Spinal Muscular Atrophy type 3 patientsJOURNAL OF CELLULAR AND MOLECULAR MEDICINE, 2020, 24 (05) : 3034 - 3039Faravelli, Irene论文数: 0 引用数: 0 h-index: 0机构: Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyMeneri, Megi论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ca Granda Osped Maggiore Policlin, Neurol Unit, Via Francesco Sforza 35, I-20122 Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalySaccomanno, Domenica论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ca Granda Osped Maggiore Policlin, Neurol Unit, Via Francesco Sforza 35, I-20122 Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyVelardo, Daniele论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ca Granda Osped Maggiore Policlin, Neurol Unit, Via Francesco Sforza 35, I-20122 Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, Italy论文数: 引用数: h-index:机构:Gagliardi, Delia论文数: 0 引用数: 0 h-index: 0机构: Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyParente, Valeria论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ca Granda Osped Maggiore Policlin, Neurol Unit, Via Francesco Sforza 35, I-20122 Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, Italy论文数: 引用数: h-index:机构:Ronchi, Dario论文数: 0 引用数: 0 h-index: 0机构: Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyStocchetti, Nino论文数: 0 引用数: 0 h-index: 0机构: Milan Univ, Dept Physiopathol & Transplantat, Fdn IRCCS Ca Granda Osped Maggiore Policlin, Milan, Italy Neuro ICU, Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyCalderini, Edoardo论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ca Granda Osped Maggiore Policlin, Mother & Child Anaesthesia & Emergency Dept, Pediat Intens Care Unit, Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyD'Angelo, Grazia论文数: 0 引用数: 0 h-index: 0机构: Sci Inst IRCCS E Medea, Lecce, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyChidini, Giovanna论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ca Granda Osped Maggiore Policlin, Mother & Child Anaesthesia & Emergency Dept, Pediat Intens Care Unit, Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyPrandi, Edi论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ca Granda Osped Maggiore Policlin, Mother & Child Anaesthesia & Emergency Dept, Pediat Intens Care Unit, Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyRicci, Giulia论文数: 0 引用数: 0 h-index: 0机构: Univ Pisa, Dept Clin & Expt Med, Neurol Clin, Pisa, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalySiciliano, Gabriele论文数: 0 引用数: 0 h-index: 0机构: Univ Pisa, Dept Clin & Expt Med, Neurol Clin, Pisa, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, Italy论文数: 引用数: h-index:机构:Comi, Giacomo Pietro论文数: 0 引用数: 0 h-index: 0机构: Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, Italy Fdn IRCCS Ca Granda Osped Maggiore Policlin, Neuromuscular & Rare Dis Unit, Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyCorti, Stefania论文数: 0 引用数: 0 h-index: 0机构: Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, Italy Fdn IRCCS Ca Granda Osped Maggiore Policlin, Neurol Unit, Via Francesco Sforza 35, I-20122 Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, ItalyMagri, Francesca论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ca Granda Osped Maggiore Policlin, Neuromuscular & Rare Dis Unit, Milan, Italy Univ Milan, Dino Ferrari Ctr, Dept Pathophysiol & Transplantat DEPT, Milan, Italy论文数: 引用数: h-index:机构:
- [22] Muscle MRI findings in spinal muscular atrophy type 3NEUROMUSCULAR DISORDERS, 2017, 27 : S122 - S122Karasoy, H.论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Med Fac, Bornova, Turkey Ege Univ, Med Fac, Bornova, TurkeyOzkan, T.论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Med Fac, Bornova, Turkey Ege Univ, Med Fac, Bornova, TurkeyArgin, M.论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Med Fac, Bornova, Turkey Ege Univ, Med Fac, Bornova, TurkeyYuceyar, A.论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Med Fac, Bornova, Turkey Ege Univ, Med Fac, Bornova, TurkeyEkmekci, O.论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Med Fac, Bornova, Turkey Ege Univ, Med Fac, Bornova, Turkey
- [23] Nonrespiratory complications of nusinersen-treated spinal muscular atrophy type 1 patientsPEDIATRIC PULMONOLOGY, 2022, 57 (03) : 686 - 694Lavie, Moran论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, IsraelRochman, Mika论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, IsraelSagi, Liora论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Pediat Neurol Inst, Tel Aviv Sourasky Med Ctr,Dana Dwek Childrens Hos, Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, IsraelFeler, Anat Yerushalmy论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Tel Aviv Sourasky Med Ctr, Pediat Gastroenterol Unit,Dana Dwek Childrens Hos, Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, IsraelOvadia, Dror论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Orthoped Dept,Tel Aviv Sourasky Med Ctr, Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, IsraelCahal, Michal论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, IsraelBe'er, Moria论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, IsraelSadot, Efraim论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Intens Care Unit,Tel Aviv Sourasky Med Ctr, Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, IsraelFattal-Valevski, Aviva论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Pediat Neurol Inst, Tel Aviv Sourasky Med Ctr,Dana Dwek Childrens Hos, Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, IsraelAmirav, Israel论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, Israel Tel Aviv Univ, Sackler Fac Med, Dana Dwek Childrens Hosp, Pediat Pulmonol Unit,Tel Aviv Sourasky Med Ctr, 6 Weizman St, IL-6423906 Tel Aviv, Israel
- [24] Nusinersen treatment in a type 3 spinal muscular atrophy patient during early pregnancyNEUROLOGICAL SCIENCES, 2023, 44 (5) : 1803 - 1804Schon, Miguel论文数: 0 引用数: 0 h-index: 0机构: Ctr Hospr Univ Lisboa Norte, Hosp Santa Maria, Dept Neurosci & Mental Hlth, Ave Prof Egas Moniz, P-1649028 Lisbon, Portugal Ctr Hospr Univ Lisboa Norte, Hosp Santa Maria, Dept Neurosci & Mental Hlth, Ave Prof Egas Moniz, P-1649028 Lisbon, PortugalDomingues, Sara论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Dept Phys Med & Rehabil, Lisbon, Portugal Ctr Hospr Univ Lisboa Norte, Hosp Santa Maria, Dept Neurosci & Mental Hlth, Ave Prof Egas Moniz, P-1649028 Lisbon, Portugalde Carvalho, Mamede论文数: 0 引用数: 0 h-index: 0机构: Ctr Hospr Univ Lisboa Norte, Hosp Santa Maria, Dept Neurosci & Mental Hlth, Ave Prof Egas Moniz, P-1649028 Lisbon, Portugal Univ Lisbon, Inst Physiol, Fac Med, Inst Med Mol JLA, Lisbon, Portugal Ctr Hospr Univ Lisboa Norte, Hosp Santa Maria, Dept Neurosci & Mental Hlth, Ave Prof Egas Moniz, P-1649028 Lisbon, Portugal论文数: 引用数: h-index:机构:
- [25] Clinical and Electropthysiological outcomes of Spinal Muscular Atrophy type 1 patients treated with NusinersenNEUROLOGY, 2019, 92 (15)Kern-Smith, Emily论文数: 0 引用数: 0 h-index: 0机构: Emory Univ, Pediat Neurol, Atlanta, GA 30322 USA Childrens Healthcare Atlanta, Pediat Neurol, Atlanta, GA USA Emory Univ, Pediat Neurol, Atlanta, GA 30322 USA论文数: 引用数: h-index:机构:
- [26] Clinical outcomes in patients with spinal muscular atrophy type 1, 2 or 3 after 1 year of nusinersen therapyNEUROMUSCULAR DISORDERS, 2019, 29 : S188 - S188Waldrop, M.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USALowes, L.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USAToops, J.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USAAlfano, L.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USAMiller, N.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USAIammarino, M.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USAKotha, K.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USAPaul, G.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USAMoore-Clingenpeel, M.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USATsao, C.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USANoritz, G.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USAShell, R.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USAFlanigan, K.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Nationwide Childrens Hosp, Columbus, OH USA
- [27] Long-term CSF responses in adult patients with spinal muscular atrophy type 2 or 3 on treatment with nusinersenJOURNAL OF NEUROLOGY, 2025, 272 (04)Cebulla, Gina论文数: 0 引用数: 0 h-index: 0机构: German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, Germany Heidelberg Univ Hosp, Natl Ctr Tumor Dis, Dept Neurol, Neurol & Neurooncol Program, Neuenheimer Feld 400, D-69120 Heidelberg, Germany German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, GermanyHai, Ling论文数: 0 引用数: 0 h-index: 0机构: German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, Germany Heidelberg Univ Hosp, Natl Ctr Tumor Dis, Dept Neurol, Neurol & Neurooncol Program, Neuenheimer Feld 400, D-69120 Heidelberg, Germany German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, GermanyWarnken, Uwe论文数: 0 引用数: 0 h-index: 0机构: German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, Germany German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, GermanyGuengoer, Cansu论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Dept Neurol, Neuenheimer Feld 400, D-69120 Heidelberg, Germany German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, GermanyHoffmann, Dirk C.论文数: 0 引用数: 0 h-index: 0机构: German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, Germany Heidelberg Univ Hosp, Natl Ctr Tumor Dis, Dept Neurol, Neurol & Neurooncol Program, Neuenheimer Feld 400, D-69120 Heidelberg, Germany German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, GermanyKorporal-Kuhnke, Mirjam论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Dept Neurol, Neuenheimer Feld 400, D-69120 Heidelberg, Germany German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, GermanyWildemann, Brigitte论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Dept Neurol, Neuenheimer Feld 400, D-69120 Heidelberg, Germany German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, Germany论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Weiler, Markus论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Dept Neurol, Neuenheimer Feld 400, D-69120 Heidelberg, Germany German Canc Res Ctr, Clin Cooperat Unit Neurooncol, German Canc Consortium DKTK, Heidelberg, Germany
- [28] Efficacy of nusinersen in type 1, 2 and 3 spinal muscular atrophy: Real world data from Hungarian patientsEUROPEAN JOURNAL OF PAEDIATRIC NEUROLOGY, 2020, 27 : 37 - 42Szabo, Lena论文数: 0 引用数: 0 h-index: 0机构: Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryGergely, Anita论文数: 0 引用数: 0 h-index: 0机构: Bethesda Childrens Hosp, 3 Bethesda St, H-1146 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryJakus, Rita论文数: 0 引用数: 0 h-index: 0机构: Bethesda Childrens Hosp, 3 Bethesda St, H-1146 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryFogarasi, Andras论文数: 0 引用数: 0 h-index: 0机构: Bethesda Childrens Hosp, 3 Bethesda St, H-1146 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryGrosz, Zoltan论文数: 0 引用数: 0 h-index: 0机构: Semmelweis Univ, Inst Genom Med & Rare Disorders, 78 Ulloi St, H-1083 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryMolnar, Maria Judit论文数: 0 引用数: 0 h-index: 0机构: Semmelweis Univ, Inst Genom Med & Rare Disorders, 78 Ulloi St, H-1083 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryAndor, Ildiko论文数: 0 引用数: 0 h-index: 0机构: Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungarySchulcz, Orsolya论文数: 0 引用数: 0 h-index: 0机构: Bethesda Childrens Hosp, 3 Bethesda St, H-1146 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryGoschler, Adam论文数: 0 引用数: 0 h-index: 0机构: Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryMedveczky, Erika论文数: 0 引用数: 0 h-index: 0机构: New St Johns Hosp & Clin, North Cent Buda Ctr, 5-9 Bolyai St, H-1023 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryCzovek, Dorottya论文数: 0 引用数: 0 h-index: 0机构: Semmelweis Univ, Dept Paediat 1, 53-54 Bokay Janos St, H-1083 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, HungaryHerczegfalvi, Agnes论文数: 0 引用数: 0 h-index: 0机构: Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, Hungary Semmelweis Univ, Dept Paediat 2, 7-9 Tuzolto St, H-1094 Budapest, Hungary
- [29] Effect of Aggressive Therapies on Spinal Muscular Atrophy Type 1 Patients Receiving NusinersenNEUROLOGY, 2019, 92 (15)Tiongson, Emmanuelle论文数: 0 引用数: 0 h-index: 0机构: Div Neurol, Los Angeles, CA USA Univ Southern Calif, Keck Sch Med, Los Angeles, CA USA Div Neurol, Los Angeles, CA USACowell, Melissa论文数: 0 引用数: 0 h-index: 0机构: Div Hosp Med, Los Angeles, CA USA Univ Southern Calif, Keck Sch Med, Los Angeles, CA USA Div Neurol, Los Angeles, CA USAKitabjian, Anna论文数: 0 引用数: 0 h-index: 0机构: Div Hosp Med, Los Angeles, CA USA Div Neurol, Los Angeles, CA USAGillett, Emily论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Pulmonol, Los Angeles, CA 90027 USA Univ Southern Calif, Keck Sch Med, Los Angeles, CA USA Div Neurol, Los Angeles, CA USALew, Cheryl论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Pulmonol, Los Angeles, CA 90027 USA Univ Southern Calif, Keck Sch Med, Los Angeles, CA USA Div Neurol, Los Angeles, CA USARamos-Platt, Leigh论文数: 0 引用数: 0 h-index: 0机构: Div Neurol, Los Angeles, CA USA Univ Southern Calif, Keck Sch Med, Los Angeles, CA USA Div Neurol, Los Angeles, CA USA
- [30] Nusinersen for Type 1 Spinal Muscular Atrophy: A Father's PerspectivePEDIATRICS, 2019, 144 (04)Hoot, Nathan R.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Hlth Sci Ctr Houston, McGovern Med Sch, Dept Emergency Med, 6431 Fannin St,4th Floor JJL, Houston, TX 77030 USA Univ Texas Hlth Sci Ctr Houston, McGovern Med Sch, Dept Emergency Med, 6431 Fannin St,4th Floor JJL, Houston, TX 77030 USA