Restoring splicing defects by antisense oligonucleotide therapy

被引:0
|
作者
Collin, R. W. [1 ]
机构
[1] Radboud Univ Nijmegen, Med Ctr, Nijmegen, Netherlands
关键词
D O I
暂无
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
S03.3
引用
收藏
页码:1050 / 1051
页数:2
相关论文
共 50 条
  • [21] OSTEOARTHRITIS A new antisense oligonucleotide therapy?
    Bernard, Nicholas J.
    NATURE REVIEWS RHEUMATOLOGY, 2018, 14 (12) : 685 - 685
  • [22] Antisense oligonucleotide therapy for neurodegenerative disease
    Smith, Richard A.
    Miller, Timothy M.
    Yamanaka, Koji
    Monia, Brett P.
    Condon, Thomas F.
    Hung, Gene
    Lobsiger, Christian S.
    Ward, Chris M.
    McAlonis-Downes, Melissa
    Wei, Hongbing
    Wancewicz, Ed V.
    Bennett, C. Frank
    Cleveland, Don W.
    JOURNAL OF CLINICAL INVESTIGATION, 2006, 116 (08): : 2290 - 2296
  • [23] Antisense Oligonucleotide Therapy for Lafora Disease
    Ahonen, Saija
    Grossman, Tamar
    Turnbull, Julie
    Kordasiewicz, Holly
    Katz, Melanie
    McCaleb, Michael
    Wang, Peixiang
    Zhao, Xiaochu
    Minassian, Berge
    NEUROLOGY, 2018, 90
  • [24] Antisense Oligonucleotide-Based Rescue of Aberrant Splicing Defects Caused by 15 Pathogenic Variants in ABCA4
    Tomkiewicz, Tomasz Z.
    Suarez-Herrera, Nuria
    Cremers, Frans P. M.
    Collin, Rob W. J.
    Garanto, Alejandro
    INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2021, 22 (09)
  • [25] Peptide-oligonucleotide hybrids in antisense therapy
    Pierce, TL
    White, AR
    Tregear, GW
    Sexton, PM
    MINI-REVIEWS IN MEDICINAL CHEMISTRY, 2005, 5 (01) : 41 - 55
  • [26] Carbohydrate modifications in antisense oligonucleotide therapy.
    Manoharan, M
    ABSTRACTS OF PAPERS OF THE AMERICAN CHEMICAL SOCIETY, 2000, 219 : U245 - U246
  • [27] Antisense oligonucleotide exon skipping therapy for DMD
    Wood, M. J. A.
    NEUROMUSCULAR DISORDERS, 2011, 21 (9-10) : 702 - 702
  • [28] Antisense Oligonucleotide Therapy for Inherited Retinal Dystrophies
    Gerard, Xavier
    Garanto, Alejandro
    Rozet, Jean-Michel
    Collin, Rob W. J.
    RETINAL DEGENERATIVE DISEASES: MECHANISMS AND EXPERIMENTAL THERAPY, 2016, 854 : 517 - 524
  • [29] Antisense oligonucleotide therapy in the management of bladder cancer
    So, A
    Rocchi, P
    Gleave, M
    CURRENT OPINION IN UROLOGY, 2005, 15 (05) : 320 - 327
  • [30] Antisense oligonucleotide repress telomerase activity via manipulating alternative splicing or translation
    Zhou, Junrui
    Li, Tingfang
    Geng, Xin
    Sui, Lei
    Wang, Feng
    BIOCHEMICAL AND BIOPHYSICAL RESEARCH COMMUNICATIONS, 2021, 582 : 118 - 124