Correcting neuromuscular pathogenic variants with CRISPR-Cas9 technology

被引:1
|
作者
Best, H. [1 ]
Woodman, K. [1 ]
Lek, A. [1 ]
Koczwara, K. [1 ]
Xu, E. [1 ]
Aykanat, A. [2 ]
Jiang, Y. [1 ]
Saltzman, M. [1 ]
Beggs, A. [2 ]
Lek, M. [1 ]
机构
[1] Yale Univ, New Haven, CT USA
[2] Harvard Med Sch, Boston, MA 02115 USA
关键词
D O I
10.1016/j.nmd.2019.06.025
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
O.7
引用
收藏
页码:S39 / S40
页数:2
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